IEMbase 0602: DHDDS-related dehydrodolichyl diphosphate synthase deficiency
Scope
| Field | Value |
|---|---|
| IEMbase ID | 602 |
| Nosology | 18.4.01.04 |
| Gene | DHDDS |
| External IDs | OMIM:613861; OMIM:608172; ORPHA:442835 |
| Generated mapping | CANDIDATE; EYS_Related_Retinitis_Pigmentosa.yaml |
| Candidate DisMech targets | None exact |
| Review date | 2026-07-07 |
IEMbase phenotype signal
IEMbase represents DHDDS-related dehydrodolichyl diphosphate synthase deficiency, labelled DHDDS-CDG and retinitis pigmentosa 59. The record is autosomal recessive, classified under disorders of dolichol biosynthesis and activation, has unknown treatability, and has no treatment rows.
The record has normal serum sialotransferrins as its only biochemical row. Clinical rows include retinitis pigmentosa, epilepsy, intellectual disability, ataxia, dystonia, hypotonia, micropenis, and acute renal failure.
DisMech phenotype coverage
EYS_Related_Retinitis_Pigmentosa.yaml is a false-positive generated candidate.
It models EYS/RP25, a photoreceptor structural/ciliary retinitis pigmentosa
caused by the EYS gene. It does not represent DHDDS, dolichol-pathway
dehydrodolichyl diphosphate synthase deficiency, CDG biology, or the
extra-ocular epilepsy, intellectual-disability, movement, endocrine, and renal
features in IEMbase.
Other local retinitis-pigmentosa entries provide final-common photoreceptor degeneration context only. No exact DHDDS-CDG / RP59 target was identified.
Concordance and completeness
Judgement: true local gap; reject EYS-related retinitis pigmentosa as exact coverage.
The candidate captures a shared retinitis-pigmentosa phenotype but fails the gene, pathway, and multisystem checks. IEMbase 0602 is a dolichol-biosynthesis CDG/retinal-neurologic disease, not an EYS photoreceptor structural disorder.
Curation actions
- Create or identify an exact DHDDS-CDG / retinitis pigmentosa 59 target before import.
- Reject
EYS_Related_Retinitis_Pigmentosa.yamlas an exact mapping. - Preserve normal sialotransferrins, retinitis pigmentosa, epilepsy, intellectual disability, ataxia, dystonia, hypotonia, micropenis, and acute renal-failure prompts.