IEMbase 0425: LRPPRC-related Leigh syndrome with French-Canadian ethnicity
Scope
| Field | Value |
|---|---|
| IEMbase ID | 425 |
| Nosology | 7.4.08.02 |
| Gene | LRPPRC |
| External IDs | OMIM:220111; ORPHA:70472 |
| Generated mapping | UNMAPPED; low candidate Leigh_Syndrome.yaml |
| Candidate DisMech targets | Leigh_Syndrome.yaml#French-Canadian |
| Review date | 2026-07-07 |
IEMbase phenotype signal
IEMbase represents LRPPRC-related Leigh syndrome with French-Canadian ethnicity, abbreviated LSFC. It records autosomal recessive inheritance. The biochemical signal is markedly increased plasma lactate and low-to-normal glucose. Clinical rows include Leigh-like MRI lesions, developmental delay, psychomotor retardation, hypotonia, ataxia, encephalopathy, liver steatosis, feeding difficulty, failure to thrive, seizures, tremor, perinatal death, and mild facial dysmorphism with Saguenay/French-Canadian founder context.
DisMech phenotype coverage
The generated unmapped status is a false negative. Local Leigh_Syndrome.yaml
has a French-Canadian subtype with MONDO congenital lactic acidosis,
Saguenay-Lac-Saint-Jean type, explicitly described as biallelic LRPPRC variants
causing complex IV-deficient Leigh syndrome. The same file also has an LRPPRC
genetic section linking biallelic LRPPRC variants to French-Canadian LSFC.
Local DisMech is stronger for the general Leigh syndrome pathophysiology and for placing LRPPRC in the complex IV/cytochrome c oxidase deficient Leigh branch. IEMbase adds a compact age-banded phenotype checklist, especially liver steatosis, dysmorphism, EEG burst-suppression, tremor, and founder-population clinical details.
Concordance and completeness
Judgement: false negative; resolve to Leigh_Syndrome.yaml#French-Canadian.
The resources agree on LRPPRC, autosomal recessive LSFC, French-Canadian / Saguenay-Lac-Saint-Jean context, complex IV-deficient Leigh syndrome, lactic acidosis, hypotonia, ataxia, encephalopathy, Leigh-like lesions, and early mortality risk.
Curation actions
- Map this record to the French-Canadian subtype in
Leigh_Syndrome.yaml. - Consider adding IEMbase's liver steatosis, EEG burst-suppression, dysmorphic features, tremor, and low/normal glucose prompts after source verification.
- Preserve LSFC as a subtype within the broader Leigh syndrome entry unless a future split creates a dedicated LRPPRC LSFC file.