IEMbase 0482: SLC5A1-related intestinal sodium-glucose cotransporter 1 deficiency
Scope
| Field | Value |
|---|---|
| IEMbase ID | 482 |
| Nosology | 3.6.04.01 |
| Gene | SLC5A1 |
| External IDs | OMIM:606824; ORPHA:35710 |
| Generated mapping | UNMAPPED; best candidate Glycogen_Storage_Disease_Type_I.yaml |
| Candidate DisMech targets | Glucose-Galactose_Malabsorption.yaml; rejected lexical candidate Glycogen_Storage_Disease_Type_I.yaml |
| Review date | 2026-07-07 |
IEMbase phenotype signal
IEMbase represents autosomal recessive SLC5A1-related intestinal sodium-glucose cotransporter 1 deficiency as glucose-galactose malabsorption. It records fructose-based carbohydrate-free formula as treatment. Biochemical rows include normal oral fructose loading, positive oral glucose and galactose loading tests, decreased glucose and galactose uptake by enterocytes, normal-to-increased urinary glucose, increased stool reducing sugars, and normal-to-high plasma sodium. Clinical rows include failure to thrive and urolithiasis.
DisMech phenotype coverage
Glucose-Galactose_Malabsorption.yaml is the exact local target. The entry
models biallelic SLC5A1/SGLT1 loss of function in small-intestinal enterocytes,
failure of active glucose/galactose absorption, spared fructose absorption via
GLUT5, osmotic diarrhea and dehydration, dietary rechallenge recurrence,
neonatal-onset watery diarrhea, hypernatremic dehydration, failure to thrive,
abdominal distension/bloating, nephrolithiasis, elevated stool reducing
substances, positive hydrogen breath testing, and fructose-based
glucose/galactose-free formula.
Concordance and completeness
Judgement: false negative generated mapping; resolve to
Glucose-Galactose_Malabsorption.yaml.
The GSD I candidate is a false-positive carbohydrate-metabolism neighbor. IEMbase and DisMech agree on SLC5A1/SGLT1 identity, recessive inheritance, selective glucose/galactose malabsorption with fructose sparing, stool reducing substances, failure to thrive, stone risk, and fructose-based formula. IEMbase adds explicit oral loading-test and enterocyte uptake rows, urinary glucose, and plasma sodium. DisMech is stronger on the causal diarrhea/dehydration path and on the distinction from renal SLC5A2/SGLT2 disease.
Curation actions
- Treat this as covered by
Glucose-Galactose_Malabsorption.yaml. - Reject
Glycogen_Storage_Disease_Type_I.yamlas an exact mapping. - Consider evidence-backed additions for the oral glucose/galactose/fructose loading tests, enterocyte uptake assays, urinary glucose, and plasma sodium.