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IEMbase 0375: CETP-related cholesteryl ester transfer protein deficiency

Scope

Field Value
IEMbase ID 375
Nosology 15.4.26.01
Gene CETP
External IDs OMIM:607322; OMIM:143470; ORPHA:79506
Generated mapping UNMAPPED; low candidate Cholesteryl_Ester_Storage_Disease.yaml
Candidate DisMech targets No exact local target
Review date 2026-07-07

IEMbase phenotype signal

IEMbase represents CETP-related cholesteryl ester transfer protein deficiency, also listed as familial hyperalphalipoproteinemia type 1 and CETP deficiency. Inheritance is autosomal dominant.

The cached record has no clinical rows or treatment rows. Biochemical rows include serum cholesterol, plasma HDL cholesterol, and serum triglyceride.

DisMech phenotype coverage

There is no exact local DisMech target for CETP deficiency. The generated low candidate Cholesteryl_Ester_Storage_Disease.yaml is a lexical false positive: that file models LIPA-related lysosomal acid lipase deficiency with lysosomal storage of cholesteryl esters and triglycerides in hepatocytes and macrophages. It does not model CETP-mediated transfer of cholesteryl esters between lipoprotein classes or familial hyperalphalipoproteinemia.

General hyperlipidemia content may provide lipid-metabolism context, but it does not replace a gene-specific CETP deficiency entry.

Concordance and completeness

Judgement: true local gap; reject the cholesteryl ester storage disease candidate.

The IEMbase disease is a circulating lipoprotein-transfer disorder, whereas CESD is an autosomal recessive lysosomal hydrolase deficiency caused by LIPA. The shared "cholesteryl ester" words are insufficient for disease mapping.

Curation actions

  • Keep this record unmapped until a CETP deficiency or familial hyperalphalipoproteinemia target exists.
  • Do not map to Cholesteryl_Ester_Storage_Disease.yaml.
  • If curated, include CETP, high-HDL/familial hyperalphalipoproteinemia scope, and the serum cholesterol/HDL/triglyceride biochemical pattern.