Pathophysiology Nodes

6
6 shared nodes are defined in this module.

Cell Types

2
Small-intestinal enterocyte CL:0000584 Cell Ontology (CL) Relation: this mechanism module involves this cell type This mechanism module involves Small-intestinal enterocyte (CL:0000584). CL:0000584 is a cell type from the Cell Ontology. Intestinal epithelial cell CL:0002563 Cell Ontology (CL) Relation: this mechanism module involves this cell type This mechanism module involves Intestinal epithelial cell (CL:0002563). CL:0002563 is a cell type from the Cell Ontology.

Biological Processes

5
Apical delivery of vesicular cargo GO:0016192 Gene Ontology (GO) Relation: this mechanism module involves this biological process This mechanism module involves Apical delivery of vesicular cargo (GO:0016192), qualified as loss of function. GO:0016192 is a biological process from the Gene Ontology. LOSS OF FUNCTION Establishment of enterocyte apical-basal polarity GO:0045198 Gene Ontology (GO) Relation: this mechanism module involves this biological process This mechanism module involves abnormal Establishment of enterocyte apical-basal polarity (GO:0045198). GO:0045198 is a biological process from the Gene Ontology. ABNORMAL Homotypic cell-cell adhesion GO:0034109 Gene Ontology (GO) Relation: this mechanism module involves this biological process This mechanism module involves decreased Homotypic cell-cell adhesion (GO:0034109). GO:0034109 is a biological process from the Gene Ontology. DECREASED Apical membrane protein delivery and retention GO:0072659 Gene Ontology (GO) Relation: this mechanism module involves this biological process This mechanism module involves decreased Apical membrane protein delivery and retention (GO:0072659). GO:0072659 is a biological process from the Gene Ontology. DECREASED Intestinal absorption GO:0050892 Gene Ontology (GO) Relation: this mechanism module involves this biological process This mechanism module involves decreased Intestinal absorption (GO:0050892). GO:0050892 is a biological process from the Gene Ontology. DECREASED
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Notes

This is a mechanism module, not a specific disease. It is the third of three sibling modules covering the epithelial CODE classes as the current nosology separates them (PMID:29654747), alongside diet_induced_osmotic_diarrhea (loss of a substrate-specific step handling an ingested nutrient; normal villus architecture; remits on dietary elimination) and electrolyte_transport_related_diarrhea (loss of an ion-transport step; normal villus architecture; low stool osmotic gap). The discriminator that assigns a disorder to this module rather than either sibling is the villus-to-crypt ratio: it is abnormal here and normal in both of the others, which is exactly the split PMID:29654747 draws. A disorder must not conform to this module and to either sibling for the same node. ARM SELECTION IS THE CURATOR'S FIRST DECISION. The module carries two molecularly distinct trigger arms as SEPARATE nodes - `#Loss of Apical Delivery Machinery` (MYO5B/STX3) and `#Loss of Junctional Adhesion Machinery` (EPCAM/SPINT2) - which converge on one rate-limiting node but are not interchangeable. They were originally curated as a single blended trigger; that structure let a conformer implicitly assert the other arm's lesion, so it was split to follow the separate-arm precedent of `defective_skeletal_mineralization` and `bilirubin_conjugation_transport`. A disorder must enter through exactly one arm and must NOT declare conformance to the other: MYO5B/STX3 disease and EPCAM/SPINT2 disease differ in histology (intracellular microvillus inclusions versus focal epithelial tufts), and apical vesicle delivery is intact in EpCAM disease. Note that a disorder may map more than one of its own nodes onto the central effector, because that node is deliberately coarser than the structural/functional split most conformers curate. Excluded: immune-mediated enteropathy (IPEX, autoimmune enteropathy), where epithelial damage is secondary to immune dysregulation rather than intrinsic to the enterocyte - PMID:29654747 separates epithelium-intrinsic from immune-mediated CODEs on exactly this basis; barrier injury and inflammatory villus blunting, covered by intestinal_barrier_dysfunction; and post-uptake intracellular metabolic defects such as DGAT1 deficiency, where the apical surface is intact and endoscopy is typically normal. Key disease-specific substitutions: microvillus inclusion disease substitutes MYO5B (or STX3/STXBP2) and the brush-border-loss-with-inclusions histology; congenital tufting enteropathy substitutes EpCAM (or SPINT2 acting through it) and the tuft-with-crypt-hyperplasia histology. Modules bind GO and CL terms only and do not use chemical (CHEBI) or disease (MONDO) term bindings.

Used By Disorder Entries

2

Pathograph

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Pathograph: causal mechanism network for Enterocyte Polarity and Trafficking Failure Module Interactive directed graph showing how this shared module's pathophysiology nodes connect.

Pathophysiology

6
Loss of Apical Delivery Machinery
trigger
ARM SELECTION IS THE CURATOR'S FIRST DECISION. This is the trafficking arm. Biallelic loss of the myosin Vb motor - or of syntaxin-3, the apical SNARE that receives its vesicles one step downstream - arrests delivery of recycling-endosome cargo to the apical membrane. Because basolateral cargo is mislocalized too, the defect is one of general epithelial polarity rather than of a single apical protein. A disorder entering the module through this arm must NOT declare conformance to the adhesion arm: the two are molecularly distinct and histologically distinguishable (intracellular microvillus inclusions here, focal epithelial tufts there), and conforming to both would assert a claudin-7 lesion that MYO5B disease does not have.
Small-intestinal enterocyte CL:0000584 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves Small-intestinal enterocyte, annotated with enterocyte (CL:0000584). CL:0000584 is a cell type from the Cell Ontology.
Apical delivery of vesicular cargo GO:0016192 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves Apical delivery of vesicular cargo, annotated with vesicle-mediated transport (GO:0016192), qualified as loss of function. GO:0016192 is a biological process from the Gene Ontology. LOSS OF FUNCTION Establishment of enterocyte apical-basal polarity GO:0045198 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves abnormal Establishment of enterocyte apical-basal polarity, annotated with establishment of epithelial cell apical/basal polarity (GO:0045198). GO:0045198 is a biological process from the Gene Ontology. ABNORMAL
Apical recycling endosome GO:0055037 Gene Ontology (GO) Relation: this pathophysiological event involves this cellular component This pathophysiological event involves Apical recycling endosome, annotated with recycling endosome (GO:0055037). GO:0055037 is a cellular component from the Gene Ontology.
Loss of Junctional Adhesion Machinery
trigger
ARM SELECTION IS THE CURATOR'S FIRST DECISION. This is the adhesion arm. Loss of functional EpCAM at the epithelial cell surface - by EPCAM variants, or indirectly by SPINT2 variants that unleash matriptase to degrade it - removes the anchor that recruits claudin-7 to the tight junction, destabilizing the apical junctional complex that maintains polarity and cohesion across the sheet. A disorder entering through this arm must NOT declare conformance to the trafficking arm: apical vesicle delivery is intact in EpCAM disease, and the histology is focal epithelial tufts rather than intracellular microvillus inclusions.
Intestinal epithelial cell CL:0002563 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves Intestinal epithelial cell (CL:0002563). CL:0002563 is a cell type from the Cell Ontology.
Homotypic cell-cell adhesion GO:0034109 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves decreased Homotypic cell-cell adhesion (GO:0034109). GO:0034109 is a biological process from the Gene Ontology. DECREASED
Tight junction GO:0070160 Gene Ontology (GO) Relation: this pathophysiological event involves this cellular component This pathophysiological event involves Tight junction (GO:0070160). GO:0070160 is a cellular component from the Gene Ontology.
Loss of a Functionally Polarized Absorptive Epithelial Surface
central effector
The rate-limiting, disorder-agnostic node and the key conformance target. Whichever arm is taken, the epithelium can no longer present a correctly organized apical surface to the lumen. In the trafficking arm the brush border is sparse or absent and microvilli are internalized into cytoplasmic inclusions; in the adhesion arm the sheet becomes dysplastic, with disorganized enterocytes crowding into focal tufts on a background of villous atrophy and crypt hyperplasia. The functional consequence is the same and is what matters mechanistically: the apical surface carries the brush-border hydrolases, the nutrient carriers and the ion exchangers, so losing it removes absorptive capacity across the board rather than for any one substrate or ion. This is why conforming disorders cannot be treated by eliminating a dietary constituent or by replacing an ion - there is no single missing step to bypass.
Small-intestinal enterocyte CL:0000584 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves Small-intestinal enterocyte, annotated with enterocyte (CL:0000584). CL:0000584 is a cell type from the Cell Ontology.
Apical membrane protein delivery and retention GO:0072659 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves decreased Apical membrane protein delivery and retention, annotated with protein localization to plasma membrane (GO:0072659). GO:0072659 is a biological process from the Gene Ontology. DECREASED Intestinal absorption GO:0050892 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves decreased Intestinal absorption (GO:0050892). GO:0050892 is a biological process from the Gene Ontology. DECREASED
Microvillus GO:0005902 Gene Ontology (GO) Relation: this pathophysiological event involves this cellular component This pathophysiological event involves Microvillus (GO:0005902). GO:0005902 is a cellular component from the Gene Ontology.
Abnormal Villus Architecture
effector
The histological signature of the class and its diagnostic discriminator. Unlike the digestive, absorptive and electrolyte-transport CODEs, where the villus-to-crypt ratio is normal, the enterocyte-structural disorders produce an abnormal ratio and abnormal morphology - villous atrophy in both arms, with crypt hyperplasia and focal tufts in the adhesion arm and subapical periodic-acid-Schiff-positive granules with intracytoplasmic microvillus inclusions in the trafficking arm. This node is what a biopsy-first diagnostic pathway detects, and it is the single feature that assigns a congenital diarrhea to this module rather than to either sibling.
Small-intestinal enterocyte CL:0000584 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves Small-intestinal enterocyte, annotated with enterocyte (CL:0000584). CL:0000584 is a cell type from the Cell Ontology.
Feeding-Independent Intractable Diarrhea
effector
The functional output. Profuse watery diarrhea begins in the neonatal period and, critically, continues whether the infant is fed or fasted, because the lesion is in the absorptive surface itself rather than in the handling of anything ingested. This is the property that rules out the two non-structural CODE classes at the bedside: no dietary elimination abolishes it, no enzyme replacement bypasses it, and no ion substitution reduces stool volume. In the adhesion arm the loss of tight junctions adds a secretory component and the loss of glucose transporters and disaccharidases an osmotic one, so the diarrhea is mixed rather than cleanly of either type.
Intestinal Failure and Parenteral Nutrition Dependence
consequence
The clinical output, and the most severe of the three epithelial CODE classes. Because absorptive capacity is structurally absent, enteral feeding cannot sustain the child and parenteral nutrition is required from the neonatal period. The natural history is then dominated by the complications of that dependence - intestinal-failure-associated liver disease, catheter-related sepsis, growth failure, renal impairment and metabolic bone disease. Most patients never achieve enteral autonomy, and small-bowel transplantation, which replaces the epithelium with genotypically normal donor tissue, is the only definitive treatment. Severity is nonetheless heterogeneous within the class, and in the adhesion arm some patients improve substantially over time, so transplantation is not automatically first-line.