Subcutaneous Panniculitis-like T-cell Lymphoma

Cancer MONDO:0019475 Pathograph 13 Show in embeddings browser Cutaneous T-cell lymphoma Peripheral T-cell lymphoma

Subcutaneous panniculitis-like T-cell lymphoma (SPTCL) is a rare primary cutaneous lymphoma in which clonal cytotoxic CD8-positive alpha/beta T cells infiltrate the subcutaneous fat lobule and rim individual adipocytes, producing nodules and plaques that mimic an inflammatory panniculitis. Since the 2008 EORTC classification study the term has been restricted to the alpha/beta phenotype; the gamma/delta counterpart is a separate, far more aggressive entity. SPTCL is unusual among lymphomas in having a defined germline predisposition: loss-of-function missense variants in HAVCR2, which encodes the inhibitory checkpoint receptor TIM-3, are found in a large fraction of cases and abolish TIM-3 surface expression, releasing a brake on innate immune activation. The resulting hyperinflammatory state explains the disease's defining complication, hemophagocytic lymphohistiocytosis (HLH), which is the dominant adverse prognostic factor. Outcome is otherwise good and immunosuppressive rather than cytotoxic therapy is now generally preferred first line, which - together with the striking responses to JAK inhibition seen in HAVCR2-mutant disease - has led several groups to question how much of the HAVCR2-mutant phenotype is neoplastic at all.

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1
Mappings
1
Inheritance
5
Pathophys.
2
Histopath.
6
Phenotypes
2
Gaps
13
Pathograph
1
Genes
3
Variants
5
Medical Actions
2
Differentials
1
Deep Research
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Classifications

ICD-O Morphology
Lymphoma
Harrison's Part
ONCOLOGY HEMATOLOGY DERMATOLOGY
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Mappings

MONDO
MONDO:0019475 subcutaneous panniculitis-like T-cell lymphoma
skos:exactMatch MONDO
Primary MONDO disease identifier for this entry.
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Inheritance

1
Autosomal recessive predisposition via germline HAVCR2 HP:0000007
Most patients are clinically sporadic, but the HAVCR2 predisposition behaves recessively: homozygous or compound heterozygous genotypes carry the highest risk of the HLH-complicated phenotype, while heterozygous carriage confers a smaller but measurable increase in risk. Genotype is germline, so it is present in non-tumor tissue and is relevant to family counselling and to donor selection for transplantation.
Autosomal recessive inheritance
Show evidence (2 references)
PMID:30792187 SUPPORT Human Clinical
"In conclusion, individuals harboring biallelic HAVCR2 (TIM3) germline mutations were highly susceptible to sporadic SPTCL, which was also associated with clonal somatic mutations."
States the biallelic germline requirement for the predisposition while noting that affected individuals are clinically sporadic.
PMID:37051767 SUPPORT DIRECT Human Clinical
"Using IPD from the present and the other three eligible cohorts (N=127), male sex, heterozygous and homozygous/compound heterozygous HAVCR2 mutations were associated with HLH by the adjusted odds ratio of 2.93 (95% confidence interval [CI]: 1.22-7.06), 4.77 (95% CI: 1.05-21.63) and 8.48 (95% CI:..."
Qualifies a strictly recessive model: heterozygous carriage also raises HLH risk, though less than a biallelic genotype does.
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Discussions and Knowledge Gaps

2
Is HAVCR2-mutant subcutaneous panniculitis-like T-cell lymphoma a lymphoma, or an inherited autoinflammatory disease that produces a clonal lymphocytic infiltrate?
KNOWLEDGE GAP OPEN sptcl_neoplastic_vs_inflammatory
Several observations sit uneasily with a neoplastic model. Immunosuppression outperforms cytotoxic chemotherapy; JAK inhibition produces rapid remission in genotyped patients who failed chemotherapy; some HAVCR2-mutant children have panniculitis without histologic evidence of lymphoma at all; and a patient has been described with two clonally unrelated episodes, which is hard to reconcile with a single transformed clone. The authors of two of these reports say the neoplastic nature of the condition is in question. The KB models this as a lymphoma entry because that is its classification and because clonal T-cell receptor rearrangement is a diagnostic criterion, but the mechanism nodes here deliberately place the germline immune lesion upstream of the clone rather than the reverse.
Show evidence (3 references)
PMID:32271897 SUPPORT Human Clinical
"Supporting rationale for ruxolitinib use, not more aggressive treatment, in this context, questioning this condition’s neoplastic nature."
States the question explicitly on the basis of the treatment response.
PMID:37062931 SUPPORT Human Clinical
"The excellent efficacy of ruxolitinib highlights this disease as an inflammatory condition instead of neoplastic nature and indicates novel agents targeting key inflammatory pathways as an encouraging approach for this disease entity."
An independent group drawing the same inference from the ruxolitinib response.
PMID:32285995 SUPPORT Human Clinical
"We show that mesenteric fatty tissue localization of SPTCL can be the presenting manifestation of TIM-3 deficiency, that this condition predisposes to recurrent lymphoma, and that flow cytometry is a possible screening tool."
Two clonally unrelated episodes in one patient argue for a predisposing immune defect rather than a single transformed clone.
What drives the HAVCR2 wild-type cases, which are roughly half of an unselected cohort?
KNOWLEDGE GAP OPEN sptcl_havcr2_wildtype_mechanism
The mechanism recorded in this entry starts from germline HAVCR2 loss of function, but about half of patients in an unselected national cohort have no HAVCR2 variant. Mutations in UNC13D, PIAS3 and KMT2D are reported more often in those cases, and CCR4 is upregulated in them, but no unifying mechanism has been established. The entry therefore has no upstream node for the wild-type group.
Show evidence (1 reference)
PMID:34535012 SUPPORT Human Clinical
"Mutations in UNC13D, PIAS3, and KMT2D were more frequent in HAVCR2WT SPTCLs."
Names the candidate lesions that distinguish the wild-type group without establishing a mechanism for it.

Pathophysiology

5
Germline TIM-3 Loss of Function
Germline missense variants in HAVCR2 substitute conserved residues in the extracellular immunoglobulin variable-like domain of TIM-3. The variant proteins misfold and never reach the plasma membrane, so the inhibitory receptor is functionally absent from the surface of T cells and of the myeloid cells that normally use it to damp innate activation. The geographic split between the two commonest alleles - p.Tyr82Cys on an East Asian and Polynesian founder haplotype, p.Ile97Met in European-ancestry patients - is a strong argument that these are ancestral, not somatic, lesions.
CD8-positive, alpha-beta T cell CL:0000625 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves CD8-positive, alpha-beta T cell (CL:0000625). CL:0000625 is a cell type from the Cell Ontology. macrophage CL:0000235 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves macrophage (CL:0000235). CL:0000235 is a cell type from the Cell Ontology. dendritic cell CL:0000451 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves dendritic cell (CL:0000451). CL:0000451 is a cell type from the Cell Ontology.
HAVCR2 hgnc:18437 HUGO Gene Nomenclature Committee (hgnc) Relation: this pathophysiological event involves this gene This pathophysiological event involves HAVCR2 (hgnc:18437). hgnc:18437 is a gene from the HUGO Gene Nomenclature Committee.
Genetic context HAVCR2 hgnc:18437 HUGO Gene Nomenclature Committee (hgnc) Relation: this genetic context concerns this gene This genetic context concerns HAVCR2 (hgnc:18437). hgnc:18437 is a gene from the HUGO Gene Nomenclature Committee. allele_type: MISSENSE variant_origin: GERMLINE zygosity: HOMOZYGOUS functional_impact_category: LOSS_OF_FUNCTION
Homozygous or compound heterozygous germline missense alleles; the commonest genotype reported is homozygous p.Tyr82Cys.
negative regulation of inflammatory response GO:0050728 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves negative regulation of inflammatory response (GO:0050728), qualified as loss of function. GO:0050728 is a biological process from the Gene Ontology. ⇓ LOSS OF FUNCTION
Show evidence (3 references)
PMID:30374066 SUPPORT Human Clinical
"We identify in ~60% of SPTCL cases germline, loss-of-function, missense variants altering highly conserved residues of TIM-3, c.245A>G (p.Tyr82Cys) and c.291A>G (p.Ile97Met), each with specific geographic distribution."
The discovery cohort establishing germline loss-of-function HAVCR2 variants as a defining lesion in a majority of cases.
PMID:30374066 SUPPORT In Vitro
"Both variants induce protein misfolding and abrogate TIM-3's plasma membrane expression, leading to persistent immune activation and increased production of inflammatory cytokines, including tumor necrosis factor-α and interleukin-1β, promoting HLH and SPTCL."
Functional work in the same paper showing the molecular consequence - misfolding and loss of surface TIM-3 - that makes this a loss-of-function node.
PMID:30792187 SUPPORT Human Clinical
"Ten patients harbored homozygous p.Y82C mutations, and 1 showed compound heterozygous mutations (p.Y82C and p.T101I)."
Documents the biallelic genotypes that define this node's genetic context.
Unrestrained Innate Immune Activation
With TIM-3 missing from the cell surface, myeloid cells sustain innate signalling that would normally be terminated. The measured consequence in patient material is persistent immune activation with excess production of inflammatory cytokines, notably TNF and interleukin-1 beta. Inflammasome assembly is the proposed proximal route to interleukin-1 family cytokine release; that step is inferred from TIM-3 biology rather than demonstrated directly in SPTCL tissue, and is recorded here at lower confidence than the cytokine measurements themselves.
macrophage CL:0000235 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves macrophage (CL:0000235). CL:0000235 is a cell type from the Cell Ontology. dendritic cell CL:0000451 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves dendritic cell (CL:0000451). CL:0000451 is a cell type from the Cell Ontology.
activation of innate immune response GO:0002218 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased activation of innate immune response (GO:0002218). GO:0002218 is a biological process from the Gene Ontology. ↑ INCREASED tumor necrosis factor production GO:0032640 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased tumor necrosis factor production (GO:0032640). GO:0032640 is a biological process from the Gene Ontology. ↑ INCREASED interleukin-1 beta production GO:0032611 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased interleukin-1 beta production (GO:0032611). GO:0032611 is a biological process from the Gene Ontology. ↑ INCREASED NLRP3 inflammasome complex assembly GO:0044546 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased NLRP3 inflammasome complex assembly (GO:0044546). GO:0044546 is a biological process from the Gene Ontology. ↑ INCREASED
Show evidence (2 references)
PMID:30374066 SUPPORT In Vitro
"Both variants induce protein misfolding and abrogate TIM-3's plasma membrane expression, leading to persistent immune activation and increased production of inflammatory cytokines, including tumor necrosis factor-α and interleukin-1β, promoting HLH and SPTCL."
Directly names persistent immune activation and the TNF and interleukin-1 beta excess that define this node.
PMID:37051767 SUPPORT Human Clinical
"These mutations result in misfolding of T-cell immunoglobulin and mucin-domain containing-3 (TIM-3) protein, leading to persistent immune activation and cytokine release, which are responsible for the pathogenesis of HLH."
An independent group stating the same causal link from TIM-3 misfolding to sustained immune activation and cytokine release.
Clonal Cytotoxic Alpha-Beta T-cell Expansion
A clonal population of CD3-positive, CD4-negative, CD8-positive, CD56-negative, betaF1-positive cytotoxic T cells expands and homes to subcutaneous fat. Cooperating somatic mutations in epigenetic regulators and signal transducers accompany the germline lesion. In HAVCR2 p.Tyr82Cys tumours the transcriptional program is enriched for IL6-JAK-STAT3 and for TNF signalling via NF-kappaB, which is the stated rationale for JAK inhibition.
CD8-positive, alpha-beta cytotoxic T cell CL:0000794 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves CD8-positive, alpha-beta cytotoxic T cell (CL:0000794). CL:0000794 is a cell type from the Cell Ontology.
cell surface receptor signaling pathway via JAK-STAT GO:0007259 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased cell surface receptor signaling pathway via JAK-STAT (GO:0007259). GO:0007259 is a biological process from the Gene Ontology. ↑ INCREASED canonical NF-kappaB signal transduction GO:0007249 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased canonical NF-kappaB signal transduction (GO:0007249). GO:0007249 is a biological process from the Gene Ontology. ↑ INCREASED
subcutaneous adipose tissue UBERON:0002190 Uberon multi-species anatomy ontology (UBERON) Relation: this pathophysiological event occurs in this anatomical location This pathophysiological event occurs in subcutaneous adipose tissue (UBERON:0002190). UBERON:0002190 is an anatomical location from the Uberon multi-species anatomy ontology.
Show evidence (3 references)
PMID:17934071 SUPPORT Human Clinical
"SPTL-ABs were generally confined to the subcutis, had a CD4-, CD8+, CD56-, betaF1+ phenotype, were uncommonly associated with a hemophagocytic syndrome (HPS; 17%), and had a favorable prognosis (5-year overall survival [OS]: 82%)."
Defines the immunophenotype and the subcutaneous localisation of the expanding clone.
PMID:34535012 SUPPORT Human Clinical
"At the gene expression level, HAVCR2Y82C SPTCLs were enriched in genes involved in IL6-JAK-STAT3 signaling and in tumor necrosis factor-α signaling via NF-κB."
Transcriptomic evidence for the two signalling programs annotated on this node.
PMID:30792187 SUPPORT Human Clinical
"SPTCL cells also harbored somatic mutations (6.2 per patient) that are frequently identified in genes associated with epigenetic regulation and signal transduction."
Establishes the cooperating somatic mutation burden in the neoplastic clone.
Adipocyte Rimming and Lobular Panniculitis
The histologic hallmark of the disease: atypical cytotoxic lymphocytes surround individual adipocytes in a lace-like pattern within a lobular panniculitis, with karyorrhexis and fat necrosis and without epidermal involvement. Adipocyte death is the direct tissue-level readout of T-cell-mediated cytotoxicity in this compartment.
adipocyte CL:0000136 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves adipocyte (CL:0000136). CL:0000136 is a cell type from the Cell Ontology. CD8-positive, alpha-beta cytotoxic T cell CL:0000794 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves CD8-positive, alpha-beta cytotoxic T cell (CL:0000794). CL:0000794 is a cell type from the Cell Ontology.
T cell mediated cytotoxicity GO:0001913 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased T cell mediated cytotoxicity (GO:0001913). GO:0001913 is a biological process from the Gene Ontology. ↑ INCREASED apoptotic process GO:0006915 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased apoptotic process (GO:0006915). GO:0006915 is a biological process from the Gene Ontology. ↑ INCREASED
subcutaneous adipose tissue UBERON:0002190 Uberon multi-species anatomy ontology (UBERON) Relation: this pathophysiological event occurs in this anatomical location This pathophysiological event occurs in subcutaneous adipose tissue (UBERON:0002190). UBERON:0002190 is an anatomical location from the Uberon multi-species anatomy ontology.
Show evidence (2 references)
PMID:34535012 SUPPORT Human Clinical
"Histopathologically, SPTCL is characterized by CD8-positive T cells infiltrating into subcutaneous adipose tissue, with rimmed individual fat cells in a lace-like pattern."
States the rimming pattern and the tissue compartment this node describes.
PMID:30126736 SUPPORT Human Clinical
"Histopathology typically showed a lobular panniculitis with individual adipocytes surrounded by atypical lymphocytes, usually with a CD3+, CD4-, CD8+, CD56-, TIA1 cytotoxic granule associated RNA binding protein 1-positive phenotype and high proliferation rate."
Independent confirmation of the lobular panniculitis pattern and the cytotoxic phenotype of the rimming cells.
Macrophage Hyperactivation and Hemophagocytosis
In a substantial minority of patients the innate activation described above escalates into full hemophagocytic lymphohistiocytosis, with activated macrophages engulfing blood cells in marrow, spleen and liver and a systemic cytokine excess producing fever, cytopenias, hyperferritinaemia, hypertriglyceridaemia and hypofibrinogenaemia. HLH risk tracks HAVCR2 genotype dose and is higher in children and in males.
macrophage CL:0000235 Cell Ontology (CL) Relation: this pathophysiological event involves this cell type This pathophysiological event involves macrophage (CL:0000235). CL:0000235 is a cell type from the Cell Ontology.
macrophage activation GO:0042116 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased macrophage activation (GO:0042116). GO:0042116 is a biological process from the Gene Ontology. ↑ INCREASED inflammatory response GO:0006954 Gene Ontology (GO) Relation: this pathophysiological event involves this biological process This pathophysiological event involves increased inflammatory response (GO:0006954). GO:0006954 is a biological process from the Gene Ontology. ↑ INCREASED
Show evidence (2 references)
PMID:34535012 SUPPORT Human Clinical
"HAVCR2Y82C was associated with younger age (P = .001), development of hemophagocytic lymphohistiocytosis or hemophagocytic lymphohistiocytosis-like systemic illness (P < .001), and short relapse-free survival (RFS) (P = .023)."
Links the germline genotype to the HLH endpoint in a nationwide cohort.
PMID:37051767 SUPPORT Human Clinical
"Homozygous HAVCR2Y82C mutation was more common in the presence of HLH compared with the absence (75.0% vs. 44.4%; P=0.02)."
Shows the genotype dose effect on HLH occurrence within an SPTCL cohort.

Histopathology

2
Adipocyte rimming by atypical lymphoid cells
Atypical lymphoid cells encircling individual adipocytes within the subcutaneous fat lobule. This is the defining diagnostic finding and is assessed on a deep incisional or excisional biopsy rather than a superficial punch.
Show evidence (1 reference)
PMID:37051767 SUPPORT Human Clinical
"The pathological hallmark of SPTCL is an adipocyte rimming by atypical lymphoid cells expressing CD3, CD8, T-cell intracytoplasmic antigen 1 (TIA-1) and T-cell receptor β F1 (BF1)."
States the hallmark finding and the accompanying immunophenotype.
Ki-67 hotspots among rimming CD8-positive T cells
Foci of high proliferative activity within the CD8-positive rimming infiltrate. Their presence separates SPTCL from lupus erythematosus panniculitis on a four-stain panel, and their absence argues against lymphoma.
Show evidence (1 reference)
PMID:26796503 SUPPORT Human Clinical
"Ki-67 hotspots were not identified in LEP, thus aiding the distinction of SPTCL from LEP."
Establishes the discriminatory value of the finding against the principal histologic mimic.

Pathograph

Use the checkboxes to hide or show graph categories. Hover nodes for evidence and cross-linked metadata.
Pathograph: causal mechanism network for Subcutaneous Panniculitis-like T-cell Lymphoma Interactive directed graph showing how pathophysiology mechanisms, phenotypes, genetic factors and variants, experimental models, environmental triggers, and treatments relate through causal and linked edges.

Phenotypes

6
Blood 1
Cytopenias Thrombocytopenia HP:0001873 Human Phenotype Ontology (HP) Relation: this clinical feature is this phenotype This clinical feature is Thrombocytopenia (HP:0001873). HP:0001873 is a phenotype from the Human Phenotype Ontology.
Show evidence (1 reference)
PMID:37051767 SUPPORT Human Clinical
"in clinical practice, patients with high-grade fever, cytopenias and presence of hemophagocytic activity in bone marrow (BM) can be presumptively diagnosed as having hemophagocytic syndrome (HPS)."
Records cytopenias as a core clinical feature of the hemophagocytic phase.
Immune 1
Lobular Panniculitis VERY_FREQUENT HP:0012490 Human Phenotype Ontology (HP) Relation: this clinical feature is this phenotype This clinical feature is Panniculitis (HP:0012490). HP:0012490 is a phenotype from the Human Phenotype Ontology.
Show evidence (1 reference)
PMID:37062931 SUPPORT Human Clinical
"Histopathologically, only two patients were diagnosed with SPTCL and three were reported as panniculitis with no sufficient evidence of lymphoma."
Documents panniculitis as the histologic finding, including cases where it falls short of a lymphoma diagnosis.
Integument 1
Subcutaneous Nodules and Plaques VERY_FREQUENT HP:0001482 Human Phenotype Ontology (HP) Relation: this clinical feature is this phenotype This clinical feature is Subcutaneous nodule (HP:0001482). HP:0001482 is a phenotype from the Human Phenotype Ontology.
Show evidence (2 references)
PMID:30126736 SUPPORT Human Clinical
"Patients presented with multiple nodular or plaque-like lesions preferentially affecting the legs and/or trunk."
Describes the lesion morphology and distribution recorded here.
PMID:35509196 SUPPORT Human Clinical
"SPTCL is usually presented clinically as painless subcutaneous and erythematous nodules over the trunk or extremities."
Confirms that the nodules are characteristically painless, which is part of why they are initially dismissed.
Metabolism 2
Fever HP:0001945 Human Phenotype Ontology (HP) Relation: this clinical feature is this phenotype This clinical feature is Fever (HP:0001945). HP:0001945 is a phenotype from the Human Phenotype Ontology.
Show evidence (1 reference)
PMID:37051767 SUPPORT Human Clinical
"Those incompletely fulfilling the criteria but being clinically consistent with HLH (i.e., fever, cytopenias, serum ferritin ≥500 μg/L, and the presence of hemophagocytosis in BM) were accounted for ‘HLH-like systemic illnesses’."
Names fever as a defining feature of the HLH-like systemic illness seen in these patients.
Hyperferritinemia Increased circulating ferritin concentration HP:0003281 Human Phenotype Ontology (HP) Relation: this clinical feature is this phenotype This clinical feature is Increased circulating ferritin concentration (HP:0003281). HP:0003281 is a phenotype from the Human Phenotype Ontology.
Show evidence (1 reference)
PMID:37051767 SUPPORT Human Clinical
"Those incompletely fulfilling the criteria but being clinically consistent with HLH (i.e., fever, cytopenias, serum ferritin ≥500 μg/L, and the presence of hemophagocytosis in BM) were accounted for ‘HLH-like systemic illnesses’."
Gives the explicit ferritin threshold used to define HLH-like systemic illness in this disease.
Other 1
Hemophagocytic Lymphohistiocytosis OCCASIONAL Hemophagocytosis HP:0012156 Human Phenotype Ontology (HP) Relation: this clinical feature is this phenotype This clinical feature is Hemophagocytosis (HP:0012156). HP:0012156 is a phenotype from the Human Phenotype Ontology.
Show evidence (2 references)
PMID:17934071 SUPPORT Human Clinical
"SPTL-ABs were generally confined to the subcutis, had a CD4-, CD8+, CD56-, betaF1+ phenotype, were uncommonly associated with a hemophagocytic syndrome (HPS; 17%), and had a favorable prognosis (5-year overall survival [OS]: 82%)."
Gives the 17% frequency underpinning the OCCASIONAL band for unselected alpha/beta SPTCL.
PMID:39538229 SUPPORT DIRECT Human Clinical
"86.4% harbored germline HAVCR2 mutation, either homozygous (77.3%) or heterozygous (9.1%) p.Y82C variant, while 68.2% developed HLH/HLH-like systemic illnesses."
Shows that in a paediatric, HAVCR2-enriched cohort HLH is the majority outcome, so the frequency band is population-dependent.
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Genetic Associations

1
HAVCR2
Gene: HAVCR2 hgnc:18437 HUGO Gene Nomenclature Committee (hgnc) Relation: this disease-associated gene is this gene This disease-associated gene is HAVCR2 (hgnc:18437). hgnc:18437 is a gene from the HUGO Gene Nomenclature Committee. relationship_type: SUSCEPTIBILITY variant_origin: GERMLINE
Show evidence (1 reference)
PMID:30792187 SUPPORT Human Clinical
"Consistent with a recent report, germline mutations in HAVCR2, encoding T-cell immunoglobulin mucin 3 (TIM3), were identified in 11 of 13 (85%) cases."
Independent replication of the HAVCR2 association in an Asian cohort.
Variants (3)
HAVCR2 c.245A>G p.Tyr82Cys Pathogenic
Gene: HAVCR2 hgnc:18437 HUGO Gene Nomenclature Committee (hgnc) Relation: this variant is in this gene This variant is in HAVCR2 (hgnc:18437). hgnc:18437 is a gene from the HUGO Gene Nomenclature Committee.
The commonest reported allele, carried on a probable founder chromosome in patients of East Asian and Polynesian ancestry. Causes TIM-3 misfolding and loss of plasma membrane expression.
Show evidence (1 reference)
PMID:30374066 SUPPORT Human Clinical
"The variant encoding p.Tyr82Cys TIM-3 occurs on a potential founder chromosome in patients with East Asian and Polynesian ancestry, while p.Ile97Met TIM-3 occurs in patients with European ancestry."
Establishes the founder origin and ancestry distribution of this allele.
HAVCR2 c.291A>G p.Ile97Met Pathogenic
Gene: HAVCR2 hgnc:18437 HUGO Gene Nomenclature Committee (hgnc) Relation: this variant is in this gene This variant is in HAVCR2 (hgnc:18437). hgnc:18437 is a gene from the HUGO Gene Nomenclature Committee.
The predominant allele in patients of European ancestry, with the same misfolding and trafficking defect as p.Tyr82Cys.
Show evidence (1 reference)
PMID:30374066 SUPPORT Human Clinical
"We identify in ~60% of SPTCL cases germline, loss-of-function, missense variants altering highly conserved residues of TIM-3, c.245A>G (p.Tyr82Cys) and c.291A>G (p.Ile97Met), each with specific geographic distribution."
Names the coding change and its loss-of-function classification.
HAVCR2 p.Thr101Ile Likely Pathogenic
Gene: HAVCR2 hgnc:18437 HUGO Gene Nomenclature Committee (hgnc) Relation: this variant is in this gene This variant is in HAVCR2 (hgnc:18437). hgnc:18437 is a gene from the HUGO Gene Nomenclature Committee.
A third recurrent allele, reported in compound heterozygosity with p.Tyr82Cys.
Show evidence (1 reference)
PMID:30792187 SUPPORT Human Clinical
"Ten patients harbored homozygous p.Y82C mutations, and 1 showed compound heterozygous mutations (p.Y82C and p.T101I)."
Documents p.Thr101Ile as the second allele in a compound heterozygous patient.
💊

Medical Actions

5
Corticosteroid-based Immunosuppressive Therapy
Action: PharmacotherapyNCI Thesaurus (NCIT) Relation: this treatment is this clinical intervention This treatment is Pharmacotherapy (NCIT:C15986). NCIT:C15986 is a clinical intervention from the NCI Thesaurus. NCIT:C15986
Agent: prednisone CHEBI:8382 Chemical Entities of Biological Interest (CHEBI) Relation: this treatment uses this therapeutic agent This treatment uses prednisone (CHEBI:8382). CHEBI:8382 is a therapeutic agent from Chemical Entities of Biological Interest. methotrexate CHEBI:44185 Chemical Entities of Biological Interest (CHEBI) Relation: this treatment uses this therapeutic agent This treatment uses methotrexate (CHEBI:44185). CHEBI:44185 is a therapeutic agent from Chemical Entities of Biological Interest. cyclosporin A CHEBI:4031 Chemical Entities of Biological Interest (CHEBI) Relation: this treatment uses this therapeutic agent This treatment uses cyclosporin A (CHEBI:4031). CHEBI:4031 is a therapeutic agent from Chemical Entities of Biological Interest.
Systemic corticosteroids alone or combined with low-dose methotrexate or cyclosporine A. This is now the usual first-line choice for uncomplicated cutaneous disease, and gives high complete response rates without the toxicity of anthracycline-based chemotherapy. Corticosteroid monotherapy relapses more often than corticosteroids combined with another immunoregulatory agent.
Mechanism Target:
Unrestrained Innate Immune Activation — Broad suppression of cytokine production and lymphocyte activation, which is why an immunosuppressive rather than cytotoxic strategy works in a disease driven by loss of an inhibitory checkpoint.
Show evidence (2 references)
PMID:30126736 SUPPORT Human Clinical
"Oral steroids alone or in combination with low-dose methotrexate or cyclosporine A were the most common initial treatment, achieving a complete response in 85% of the treated patients."
Gives the regimen and the complete response rate recorded here.
PMID:37840116 SUPPORT Human Clinical
"The corticosteroid monotherapy experienced a higher recurrence rate than the corticosteroids plus other immunoregulatory agents therapy (66.7 vs. 0.0%, p = 0.029)."
Supports combining corticosteroids with a second immunoregulatory agent rather than using steroids alone.
Multiagent Chemotherapy
Action: chemotherapyNCI Thesaurus (NCIT) Relation: this treatment is this clinical intervention This treatment is chemotherapy (NCIT:C15632). NCIT:C15632 is a clinical intervention from the NCI Thesaurus. Ontology label: Chemotherapy NCIT:C15632
Anthracycline-based combination chemotherapy, historically the default and now reserved for patients presenting with HLH or progressing on immunosuppression. In a paediatric comparison it achieved a numerically higher durable complete remission rate than immunosuppressive therapy but at the cost of more adverse events, and the difference in remission rate was not significant.
Show evidence (2 references)
PMID:39538229 SUPPORT DIRECT Human Clinical
"Durable complete remission (CR) was achieved in 71.4% and 50.0% after first-line chemotherapy and IST, respectively (P=0.45); however, chemotherapy tended to increase any AEs compared to IST (57.1% vs. 12.5%; P=0.07)."
Reports the efficacy and toxicity trade-off between chemotherapy and immunosuppression without establishing superiority of either.
PMID:15368328 SUPPORT Human Clinical
"Anthracycline-based chemotherapy regimens were the most commonly used and most effective systemic treatment options, producing long-term CR in approximately 30% of patients."
Documents the historical role and the durable remission rate of anthracycline-based regimens.
Ruxolitinib
Action: PharmacotherapyNCI Thesaurus (NCIT) Relation: this treatment is this clinical intervention This treatment is Pharmacotherapy (NCIT:C15986). NCIT:C15986 is a clinical intervention from the NCI Thesaurus. NCIT:C15986
Agent: ruxolitinib CHEBI:66919 Chemical Entities of Biological Interest (CHEBI) Relation: this treatment uses this therapeutic agent This treatment uses ruxolitinib (CHEBI:66919). CHEBI:66919 is a therapeutic agent from Chemical Entities of Biological Interest.
A JAK1/JAK2 inhibitor. Its use follows directly from the mechanism: TIM-3 loss drives cytokine-mediated inflammation and HAVCR2-mutant tumours are transcriptionally enriched for IL6-JAK-STAT3 signalling. Reported responses in HAVCR2-mutant children have been rapid and durable after corticosteroids, other immunosuppressants and chemotherapy had all failed.
Mechanism Target:
Clonal Cytotoxic Alpha-Beta T-cell Expansion — Blocks the JAK-STAT signalling program enriched in HAVCR2 p.Tyr82Cys tumours.
Macrophage Hyperactivation and Hemophagocytosis — Suppresses the cytokine signalling that sustains the hemophagocytic syndrome.
Show evidence (2 references)
PMID:37062931 SUPPORT Human Clinical
"All patients initially received corticosteroids, immunosuppressants or chemotherapy, achieving unfavourable responses. Strikingly, they responded well to ruxolitinib targeting inflammatory cytokines, allowing rapid disease resolution and/or long-term maintenance of remission."
Reports responses to ruxolitinib after failure of conventional therapy in genotyped patients.
PMID:32271897 SUPPORT Human Clinical
"First evidence of ruxolitinib efficacy for subcutaneous panniculitis-like T-cell lymphoma with hemophagocytic lymphohistiocytosis."
The first report of ruxolitinib activity in this indication.
Hematopoietic Stem Cell Transplantation
Action: Hematopoietic Cell TransplantationNCI Thesaurus (NCIT) Relation: this treatment is this clinical intervention This treatment is Hematopoietic Cell Transplantation (NCIT:C15431). NCIT:C15431 is a clinical intervention from the NCI Thesaurus. NCIT:C15431
Reserved for refractory or relapsed disease, particularly HLH-complicated disease. Because the predisposing HAVCR2 variant is germline, donor genotype matters: a relapse has been reported after a sibling-identical transplant from a donor who turned out to carry the same homozygous HAVCR2 mutation.
Show evidence (2 references)
PMID:37840116 SUPPORT Human Clinical
"Fifteen patients, including 5 with relapsed/refractory SPTCL-HLH, responded well and survived after receiving SCT."
Supports transplantation as an effective option in refractory disease.
PMID:37840116 SUPPORT Human Clinical
"One case who received a sibling-identical SCT relapsed. Further analysis revealed a homozygous HAVCR2 mutation with the donor."
Documents the germline-genotype pitfall in related-donor selection.
Radiation Therapy
Action: Radiation TherapyNCI Thesaurus (NCIT) Relation: this treatment is this clinical intervention This treatment is Radiation Therapy (NCIT:C15313). NCIT:C15313 is a clinical intervention from the NCI Thesaurus. NCIT:C15313
Skin-directed radiotherapy for localised or solitary lesions, avoiding systemic exposure in patients whose disease is anatomically limited.
Show evidence (1 reference)
PMID:15368328 SUPPORT INDIRECT Human Clinical
"The authors performed a systematic analysis of all patients with SPTCL reported on in the English-language medical literature, with emphasis on specific clinical features, experiences involving the use of radiotherapy and systemic agents, and prognostic factors predictive of treatment response..."
Establishes that radiotherapy is part of the reported treatment repertoire; this pooled review does not isolate its efficacy.
🔬

Diagnosis

3
Deep skin biopsy with immunophenotyping
Diagnosis rests on a deep biopsy showing lobular panniculitis with adipocyte rimming, plus an immunohistochemical panel establishing the CD3-positive, CD4-negative, CD8-positive, CD56-negative, betaF1-positive cytotoxic phenotype. Demonstrating a clonal T-cell receptor rearrangement supports the diagnosis.
Show evidence (1 reference)
PMID:30126736 SUPPORT Human Clinical
"Histopathology typically showed a lobular panniculitis with individual adipocytes surrounded by atypical lymphocytes, usually with a CD3+, CD4-, CD8+, CD56-, TIA1 cytotoxic granule associated RNA binding protein 1-positive phenotype and high proliferation rate."
Sets out the histologic and immunophenotypic criteria used in practice.
Germline HAVCR2 sequencing
Sequencing of HAVCR2 exon 2 covers the three recurrent alleles and is increasingly performed at diagnosis, particularly in children and in patients with HLH, because a positive result changes surveillance, family counselling and - if transplantation is considered - donor selection. Reduced TIM-3 surface expression by flow cytometry has been proposed as a screening test.
Show evidence (2 references)
PMID:37051767 SUPPORT Human Clinical
"The designed primer could cover pathogenic HAVCR2 variants of p.Y82C, p.I97M and p.T101I."
Confirms that exon 2 sequencing captures all three recurrent alleles.
PMID:32285995 SUPPORT Human Clinical
"We show that mesenteric fatty tissue localization of SPTCL can be the presenting manifestation of TIM-3 deficiency, that this condition predisposes to recurrent lymphoma, and that flow cytometry is a possible screening tool."
Supports flow cytometry as a screening approach and documents the recurrence risk that motivates genotyping.
FDG PET/CT for staging and response assessment
Used to define the extent of subcutaneous disease, look for extracutaneous involvement and follow treatment response.
Show evidence (1 reference)
PMID:35509196 SUPPORT Human Clinical
"Positron emission tomography scan is utilized for disease staging and treatment follow-up."
States the role of PET in staging and follow-up for this disease.
📈

Progression

2
Indolent relapsing cutaneous disease
Most patients follow a chronic, relapsing course confined to the subcutis with an excellent survival. In the EORTC series the alpha/beta phenotype was generally confined to the subcutis and had a 5-year overall survival of 82%.
Show evidence (2 references)
PMID:17934071 SUPPORT Human Clinical
"SPTL-ABs were generally confined to the subcutis, had a CD4-, CD8+, CD56-, betaF1+ phenotype, were uncommonly associated with a hemophagocytic syndrome (HPS; 17%), and had a favorable prognosis (5-year overall survival [OS]: 82%)."
Establishes both the indolent course and the baseline survival figure for the alpha/beta entity.
PMID:30126736 SUPPORT Human Clinical
"The 5-year disease-specific survival rate was 85.7%."
An independent multicentre series reporting concordant 5-year survival.
Hemophagocytic lymphohistiocytosis
A minority of patients develop HLH, either at presentation or during the course of cutaneous disease. This is the single dominant adverse prognostic event and drives most disease-related mortality.
Show evidence (2 references)
PMID:17934071 SUPPORT Human Clinical
"SPTL-AB patients without HPS had a significantly better survival than patients with HPS (5-year OS: 91% vs 46%; P<.001)."
Quantifies the survival penalty imposed by hemophagocytic syndrome.
PMID:15368328 SUPPORT Human Clinical
"The presence of HPS at diagnosis and expression of the gamma/delta T-cell receptor (TCR) by tumor cells were associated with poor survival, whereas age was not."
Identifies hemophagocytic syndrome as an adverse prognostic factor independent of age in a pooled literature analysis.
📊

Prevalence

1
Worldwide
Unknown Ultra Rare
No population-based incidence estimate exists. The only quantitative anchor in the literature is SPTCL's share of non-Hodgkin lymphoma diagnoses, which is consistently reported as under 1%.
Show evidence (1 reference)
PMID:39538229 SUPPORT Human Clinical
"Subcutaneous panniculitis-like T-cell lymphoma (SPTCL) is a distinctive subtype of T-cell non-Hodgkin lymphoma (NHL), accounting for <1% of all NHL cases worldwide"
Gives the only widely reported frequency figure, expressed as a fraction of NHL rather than as a population rate.
🌍

Epidemiology

2
Female predominance
A consistent female excess across independent cohorts: a female-to-male ratio of 1.7 in a European multicentre series and 69.8% women in a Korean national cohort. Two unrelated populations agreeing on roughly 70% female makes this a first-order feature of the disease rather than a cohort artefact, and it is one of the things that distinguishes SPTCL from most peripheral T-cell lymphomas.
Show evidence (2 references)
PMID:30126736 SUPPORT Human Clinical
"The female-to-male ratio was 1.7. The median age at diagnosis was 46.5 years."
Gives the sex ratio and median age in a European multicentre series.
PMID:34535012 SUPPORT Human Clinical
"The median age at diagnosis was 32 years (range, 8-74 years), and 37 (69.8%) patients were women."
Independent confirmation of the female excess in a Korean national cohort, with a younger median age.
Age at diagnosis
Median age at diagnosis differs markedly between cohorts - 46.5 years in a European series against 32 years in a Korean national cohort. Two explanations are available and this entry does not choose between them: the p.Tyr82Cys allele is associated with younger onset, and it is also far commoner in East Asian populations. They are confounded and cannot be separated by these data, because the cohort with the younger median is the one with the founder allele and neither series stratifies the other's variable. The reported range spans childhood to old age.
median 32 years (Korean national cohort) to 46.5 years (European multicentre series) years
The range recorded here is the Korean national cohort's, which is the only one of the cited series to report one explicitly.
Show evidence (2 references)
PMID:34535012 SUPPORT Human Clinical
"The median age at diagnosis was 32 years (range, 8-74 years), and 37 (69.8%) patients were women."
Gives the median and range recorded here.
PMID:34535012 SUPPORT Human Clinical
"HAVCR2Y82C was associated with younger age (P = .001), development of hemophagocytic lymphohistiocytosis or hemophagocytic lymphohistiocytosis-like systemic illness (P < .001), and short relapse-free survival (RFS) (P = .023)."
Supports attributing the between-cohort age difference to genotype rather than to geography alone.
🔀

Differential Diagnoses

2

Conditions with similar clinical presentations that must be differentiated from Subcutaneous Panniculitis-like T-cell Lymphoma:

Lupus erythematosus panniculitis
Overlapping Features The principal histologic mimic. The two overlap clinically and histologically and can coexist in the same patient, but SPTCL carries the risk of HLH and so the distinction matters. Molecular profiling separates them, and overlapping cases cluster with lupus panniculitis rather than with SPTCL.
Distinguishing Features
  • Ki-67 hotspots enriched in atypical CD8-positive T cells are present in SPTCL and absent in lupus panniculitis
  • Clonal T-cell receptor rearrangement favours SPTCL
  • Gene expression profiling separates the two entities, with overlap cases resembling lupus panniculitis
Show evidence (2 references)
PMID:26796503 SUPPORT Human Clinical
"Lymphocyte atypia combined with adipocyte rimming of CD8+ T cells within Ki-67 hotspots was also highly specific for the diagnosis of SPTCL."
Provides the specific histologic combination that discriminates the two.
PMID:33966586 SUPPORT Human Clinical
"Gene expression unsupervised analysis of the samples differentiated SPTCL from LEP samples. Most overlapping cases were clustered with LEP cases."
Molecular evidence that the entities are separable and that overlap cases behave like lupus panniculitis.
Primary cutaneous gamma-delta T-cell lymphoma
Overlapping Features Formerly grouped with SPTCL under a single label. It carries a gamma/delta rather than alpha/beta receptor, frequently involves the epidermis and ulcerates, and has a far worse outcome irrespective of treatment. Separating the two on betaF1 and TCR-delta staining is the reason the term SPTCL is now restricted to the alpha/beta entity.
Distinguishing Features
  • CD4-negative, CD8-negative, CD56 variable, betaF1-negative phenotype
  • Frequent epidermal or dermal involvement and ulceration rather than disease confined to the subcutis
  • 5-year overall survival of 11% versus 82% for the alpha/beta entity
Show evidence (2 references)
PMID:17934071 SUPPORT Human Clinical
"SPTL-GDs often showed (epi)dermal involvement and/or ulceration, a CD4-, CD8-, CD56+/-, betaF1- T-cell phenotype, and poor prognosis (5-year OS: 11%), irrespective of the presence of HPS or type of treatment."
Gives the phenotype, distribution and outcome that separate the gamma/delta entity.
PMID:17934071 SUPPORT Human Clinical
"These results indicate that SPTL-AB and SPTL-GD are distinct entities, and justify that the term SPTL should further be used only for SPTL-AB."
The nomenclature decision that makes this a differential rather than a subtype.
{ }

Source YAML

click to show
name: Subcutaneous Panniculitis-like T-cell Lymphoma
creation_date: "2026-08-29T15:30:00Z"
category: Cancer
categories:
- Hematologic Malignancy
- T-cell Neoplasm
- Cutaneous Lymphoma
synonyms:
- SPTCL
- subcutaneous panniculitic T-cell lymphoma
- T-CELL LYMPHOMA, SUBCUTANEOUS PANNICULITIS-LIKE
- subcutaneous panniculitis-like T-cell lymphoma, Alpha/Beta type
- SPTL-AB
description: >-
  Subcutaneous panniculitis-like T-cell lymphoma (SPTCL) is a rare primary
  cutaneous lymphoma in which clonal cytotoxic CD8-positive alpha/beta T cells
  infiltrate the subcutaneous fat lobule and rim individual adipocytes,
  producing nodules and plaques that mimic an inflammatory panniculitis. Since
  the 2008 EORTC classification study the term has been restricted to the
  alpha/beta phenotype; the gamma/delta counterpart is a separate, far more
  aggressive entity. SPTCL is unusual among lymphomas in having a defined
  germline predisposition: loss-of-function missense variants in HAVCR2, which
  encodes the inhibitory checkpoint receptor TIM-3, are found in a large
  fraction of cases and abolish TIM-3 surface expression, releasing a brake on
  innate immune activation. The resulting hyperinflammatory state explains the
  disease's defining complication, hemophagocytic lymphohistiocytosis (HLH),
  which is the dominant adverse prognostic factor. Outcome is otherwise good
  and immunosuppressive rather than cytotoxic therapy is now generally
  preferred first line, which - together with the striking responses to
  JAK inhibition seen in HAVCR2-mutant disease - has led several groups to
  question how much of the HAVCR2-mutant phenotype is neoplastic at all.
disease_term:
  preferred_term: subcutaneous panniculitis-like T-cell lymphoma
  term:
    id: MONDO:0019475
    label: subcutaneous panniculitis-like T-cell lymphoma
mappings:
  mondo_mappings:
  - term:
      id: MONDO:0019475
      label: subcutaneous panniculitis-like T-cell lymphoma
    mapping_predicate: skos:exactMatch
    mapping_source: MONDO
    mapping_justification: Primary MONDO disease identifier for this entry.
parents:
- Cutaneous T-cell lymphoma
- Peripheral T-cell lymphoma
classifications:
  harrisons_chapter:
  - classification_value: ONCOLOGY_HEMATOLOGY
    notes: >-
      A mature T-cell non-Hodgkin lymphoma; staging, prognosis and systemic
      therapy follow lymphoma practice.
  - classification_value: DERMATOLOGY
    notes: >-
      Disease is confined to the skin and subcutis in most patients and is
      diagnosed on deep skin biopsy.
  icdo_morphology:
    classification_value: Lymphoma
    evidence:
    - reference: PMID:39538229
      reference_title: "Characteristics and therapeutic outcomes of subcutaneous panniculitis-like T-cell lymphoma with and without germline HAVCR2 mutations in Thai children and adolescents."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "Subcutaneous panniculitis-like T-cell lymphoma (SPTCL) is a distinctive subtype of T-cell non-Hodgkin lymphoma (NHL), accounting for <1% of all NHL cases worldwide"
      explanation: >-
        Places SPTCL within the non-Hodgkin lymphoma family, supporting the
        ICD-O lymphoma morphology bucket.
inheritance:
- name: Autosomal recessive predisposition via germline HAVCR2
  description: >-
    Most patients are clinically sporadic, but the HAVCR2 predisposition
    behaves recessively: homozygous or compound heterozygous genotypes carry
    the highest risk of the HLH-complicated phenotype, while heterozygous
    carriage confers a smaller but measurable increase in risk. Genotype is
    germline, so it is present in non-tumor tissue and is relevant to family
    counselling and to donor selection for transplantation.
  inheritance_term:
    preferred_term: Autosomal recessive inheritance
    term:
      id: HP:0000007
      label: Autosomal recessive inheritance
  evidence:
  - reference: PMID:30792187
    reference_title: "Frequent germline mutations of HAVCR2 in sporadic subcutaneous panniculitis-like T-cell lymphoma."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "In conclusion, individuals harboring biallelic HAVCR2 (TIM3) germline mutations were highly susceptible to sporadic SPTCL, which was also associated with clonal somatic mutations."
    explanation: >-
      States the biallelic germline requirement for the predisposition while
      noting that affected individuals are clinically sporadic.
  - reference: PMID:37051767
    reference_title: "Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis."
    supports: SUPPORT
    directness: DIRECT
    evidence_source: HUMAN_CLINICAL
    snippet: "Using IPD from the present and the other three eligible cohorts (N=127), male sex, heterozygous and homozygous/compound heterozygous HAVCR2 mutations were associated with HLH by the adjusted odds ratio of 2.93 (95% confidence interval [CI]: 1.22-7.06), 4.77 (95% CI: 1.05-21.63) and 8.48 (95% CI: 2.98-24.10), respectively."
    explanation: >-
      Qualifies a strictly recessive model: heterozygous carriage also raises
      HLH risk, though less than a biallelic genotype does.
prevalence:
- population: Worldwide
  measure_type: UNKNOWN
  prevalence_class: ULTRA_RARE
  notes: >-
    No population-based incidence estimate exists. The only quantitative
    anchor in the literature is SPTCL's share of non-Hodgkin lymphoma
    diagnoses, which is consistently reported as under 1%.
  evidence:
  - reference: PMID:39538229
    reference_title: "Characteristics and therapeutic outcomes of subcutaneous panniculitis-like T-cell lymphoma with and without germline HAVCR2 mutations in Thai children and adolescents."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Subcutaneous panniculitis-like T-cell lymphoma (SPTCL) is a distinctive subtype of T-cell non-Hodgkin lymphoma (NHL), accounting for <1% of all NHL cases worldwide"
    explanation: >-
      Gives the only widely reported frequency figure, expressed as a fraction
      of NHL rather than as a population rate.
epidemiology:
- name: Female predominance
  description: >-
    A consistent female excess across independent cohorts: a female-to-male
    ratio of 1.7 in a European multicentre series and 69.8% women in a Korean
    national cohort. Two unrelated populations agreeing on roughly 70% female
    makes this a first-order feature of the disease rather than a cohort
    artefact, and it is one of the things that distinguishes SPTCL from most
    peripheral T-cell lymphomas.
  evidence:
  - reference: PMID:30126736
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: Clinical features, therapeutic approach, and outcome in a case series of 16 patients."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The female-to-male ratio was 1.7. The median age at diagnosis was 46.5 years."
    explanation: >-
      Gives the sex ratio and median age in a European multicentre series.
  - reference: PMID:34535012
    reference_title: "Genetic profiles of subcutaneous panniculitis-like T-cell lymphoma and clinicopathological impact of HAVCR2 mutations."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The median age at diagnosis was 32 years (range, 8-74 years), and 37 (69.8%) patients were women."
    explanation: >-
      Independent confirmation of the female excess in a Korean national cohort,
      with a younger median age.
- name: Age at diagnosis
  description: >-
    Median age at diagnosis differs markedly between cohorts - 46.5 years in a
    European series against 32 years in a Korean national cohort. Two
    explanations are available and this entry does not choose between them: the
    p.Tyr82Cys allele is associated with younger onset, and it is also far
    commoner in East Asian populations. They are confounded and cannot be
    separated by these data, because the cohort with the younger median is the
    one with the founder allele and neither series stratifies the other's
    variable. The reported range spans childhood to old age.
  minimum_value: 8.0
  maximum_value: 74.0
  mean_range: "median 32 years (Korean national cohort) to 46.5 years (European multicentre series)"
  unit: years
  notes: >-
    The range recorded here is the Korean national cohort's, which is the only
    one of the cited series to report one explicitly.
  evidence:
  - reference: PMID:34535012
    reference_title: "Genetic profiles of subcutaneous panniculitis-like T-cell lymphoma and clinicopathological impact of HAVCR2 mutations."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The median age at diagnosis was 32 years (range, 8-74 years), and 37 (69.8%) patients were women."
    explanation: >-
      Gives the median and range recorded here.
  - reference: PMID:34535012
    reference_title: "Genetic profiles of subcutaneous panniculitis-like T-cell lymphoma and clinicopathological impact of HAVCR2 mutations."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "HAVCR2Y82C was associated with younger age (P = .001), development of hemophagocytic lymphohistiocytosis or hemophagocytic lymphohistiocytosis-like systemic illness (P < .001), and short relapse-free survival (RFS) (P = .023)."
    explanation: >-
      Supports attributing the between-cohort age difference to genotype rather
      than to geography alone.
progression:
- phase: Indolent relapsing cutaneous disease
  notes: >-
    Most patients follow a chronic, relapsing course confined to the subcutis
    with an excellent survival. In the EORTC series the alpha/beta phenotype
    was generally confined to the subcutis and had a 5-year overall survival of
    82%.
  evidence:
  - reference: PMID:17934071
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: definition, classification, and prognostic factors: an EORTC Cutaneous Lymphoma Group Study of 83 cases."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "SPTL-ABs were generally confined to the subcutis, had a CD4-, CD8+, CD56-, betaF1+ phenotype, were uncommonly associated with a hemophagocytic syndrome (HPS; 17%), and had a favorable prognosis (5-year overall survival [OS]: 82%)."
    explanation: >-
      Establishes both the indolent course and the baseline survival figure for
      the alpha/beta entity.
  - reference: PMID:30126736
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: Clinical features, therapeutic approach, and outcome in a case series of 16 patients."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The 5-year disease-specific survival rate was 85.7%."
    explanation: >-
      An independent multicentre series reporting concordant 5-year survival.
- phase: Hemophagocytic lymphohistiocytosis
  notes: >-
    A minority of patients develop HLH, either at presentation or during the
    course of cutaneous disease. This is the single dominant adverse prognostic
    event and drives most disease-related mortality.
  evidence:
  - reference: PMID:17934071
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: definition, classification, and prognostic factors: an EORTC Cutaneous Lymphoma Group Study of 83 cases."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "SPTL-AB patients without HPS had a significantly better survival than patients with HPS (5-year OS: 91% vs 46%; P<.001)."
    explanation: >-
      Quantifies the survival penalty imposed by hemophagocytic syndrome.
  - reference: PMID:15368328
    reference_title: "Immunophenotypic and molecular features, clinical outcomes, treatments, and prognostic factors associated with subcutaneous panniculitis-like T-cell lymphoma: a systematic analysis of 156 patients reported in the literature."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The presence of HPS at diagnosis and expression of the gamma/delta T-cell receptor (TCR) by tumor cells were associated with poor survival, whereas age was not."
    explanation: >-
      Identifies hemophagocytic syndrome as an adverse prognostic factor
      independent of age in a pooled literature analysis.
pathophysiology:
- name: Germline TIM-3 Loss of Function
  biological_scale: MOLECULAR
  description: >-
    Germline missense variants in HAVCR2 substitute conserved residues in the
    extracellular immunoglobulin variable-like domain of TIM-3. The variant
    proteins misfold and never reach the plasma membrane, so the inhibitory
    receptor is functionally absent from the surface of T cells and of the
    myeloid cells that normally use it to damp innate activation. The
    geographic split between the two commonest alleles - p.Tyr82Cys on an East
    Asian and Polynesian founder haplotype, p.Ile97Met in European-ancestry
    patients - is a strong argument that these are ancestral, not somatic,
    lesions.
  genes:
  - preferred_term: HAVCR2
    term:
      id: hgnc:18437
      label: HAVCR2
  cell_types:
  - preferred_term: CD8-positive, alpha-beta T cell
    term:
      id: CL:0000625
      label: CD8-positive, alpha-beta T cell
  - preferred_term: macrophage
    term:
      id: CL:0000235
      label: macrophage
  - preferred_term: dendritic cell
    term:
      id: CL:0000451
      label: dendritic cell
  biological_processes:
  - preferred_term: negative regulation of inflammatory response
    modifier: LOSS_OF_FUNCTION
    term:
      id: GO:0050728
      label: negative regulation of inflammatory response
  genetic_context:
    gene:
      preferred_term: HAVCR2
      term:
        id: hgnc:18437
        label: HAVCR2
    allele_type: MISSENSE
    variant_origin: GERMLINE
    zygosity: HOMOZYGOUS
    functional_impact_category: LOSS_OF_FUNCTION
    description: >-
      Homozygous or compound heterozygous germline missense alleles; the
      commonest genotype reported is homozygous p.Tyr82Cys.
  evidence:
  - reference: PMID:30374066
    reference_title: "Germline HAVCR2 mutations altering TIM-3 characterize subcutaneous panniculitis-like T cell lymphomas with hemophagocytic lymphohistiocytic syndrome."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "We identify in ~60% of SPTCL cases germline, loss-of-function, missense variants altering highly conserved residues of TIM-3, c.245A>G (p.Tyr82Cys) and c.291A>G (p.Ile97Met), each with specific geographic distribution."
    explanation: >-
      The discovery cohort establishing germline loss-of-function HAVCR2
      variants as a defining lesion in a majority of cases.
  - reference: PMID:30374066
    reference_title: "Germline HAVCR2 mutations altering TIM-3 characterize subcutaneous panniculitis-like T cell lymphomas with hemophagocytic lymphohistiocytic syndrome."
    supports: SUPPORT
    evidence_source: IN_VITRO
    snippet: "Both variants induce protein misfolding and abrogate TIM-3's plasma membrane expression, leading to persistent immune activation and increased production of inflammatory cytokines, including tumor necrosis factor-α and interleukin-1β, promoting HLH and SPTCL."
    explanation: >-
      Functional work in the same paper showing the molecular consequence -
      misfolding and loss of surface TIM-3 - that makes this a loss-of-function
      node.
  - reference: PMID:30792187
    reference_title: "Frequent germline mutations of HAVCR2 in sporadic subcutaneous panniculitis-like T-cell lymphoma."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Ten patients harbored homozygous p.Y82C mutations, and 1 showed compound heterozygous mutations (p.Y82C and p.T101I)."
    explanation: >-
      Documents the biallelic genotypes that define this node's genetic
      context.
  downstream:
  - target: Unrestrained Innate Immune Activation
    description: >-
      Absent surface TIM-3 removes an inhibitory input on macrophages and
      dendritic cells, lowering the threshold for innate activation.
- name: Unrestrained Innate Immune Activation
  biological_scale: CELLULAR
  description: >-
    With TIM-3 missing from the cell surface, myeloid cells sustain innate
    signalling that would normally be terminated. The measured consequence in
    patient material is persistent immune activation with excess production of
    inflammatory cytokines, notably TNF and interleukin-1 beta. Inflammasome
    assembly is the proposed proximal route to interleukin-1 family cytokine
    release; that step is inferred from TIM-3 biology rather than demonstrated
    directly in SPTCL tissue, and is recorded here at lower confidence than the
    cytokine measurements themselves.
  cell_types:
  - preferred_term: macrophage
    term:
      id: CL:0000235
      label: macrophage
  - preferred_term: dendritic cell
    term:
      id: CL:0000451
      label: dendritic cell
  biological_processes:
  - preferred_term: activation of innate immune response
    modifier: INCREASED
    term:
      id: GO:0002218
      label: activation of innate immune response
  - preferred_term: tumor necrosis factor production
    modifier: INCREASED
    term:
      id: GO:0032640
      label: tumor necrosis factor production
  - preferred_term: interleukin-1 beta production
    modifier: INCREASED
    term:
      id: GO:0032611
      label: interleukin-1 beta production
  - preferred_term: NLRP3 inflammasome complex assembly
    modifier: INCREASED
    term:
      id: GO:0044546
      label: NLRP3 inflammasome complex assembly
  mechanism_confidence: PROVISIONAL
  evidence:
  - reference: PMID:30374066
    reference_title: "Germline HAVCR2 mutations altering TIM-3 characterize subcutaneous panniculitis-like T cell lymphomas with hemophagocytic lymphohistiocytic syndrome."
    supports: SUPPORT
    evidence_source: IN_VITRO
    snippet: "Both variants induce protein misfolding and abrogate TIM-3's plasma membrane expression, leading to persistent immune activation and increased production of inflammatory cytokines, including tumor necrosis factor-α and interleukin-1β, promoting HLH and SPTCL."
    explanation: >-
      Directly names persistent immune activation and the TNF and
      interleukin-1 beta excess that define this node.
  - reference: PMID:37051767
    reference_title: "Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "These mutations result in misfolding of T-cell immunoglobulin and mucin-domain containing-3 (TIM-3) protein, leading to persistent immune activation and cytokine release, which are responsible for the pathogenesis of HLH."
    explanation: >-
      An independent group stating the same causal link from TIM-3 misfolding
      to sustained immune activation and cytokine release.
  downstream:
  - target: Macrophage Hyperactivation and Hemophagocytosis
    description: >-
      Sustained innate activation escalates into the systemic macrophage
      activation syndrome recognised clinically as HLH.
  - target: Clonal Cytotoxic Alpha-Beta T-cell Expansion
    description: >-
      The chronic inflammatory milieu is the proposed context in which a
      cytotoxic T-cell clone emerges and is sustained.
- name: Clonal Cytotoxic Alpha-Beta T-cell Expansion
  biological_scale: CELLULAR
  description: >-
    A clonal population of CD3-positive, CD4-negative, CD8-positive,
    CD56-negative, betaF1-positive cytotoxic T cells expands and homes to
    subcutaneous fat. Cooperating somatic mutations in epigenetic regulators
    and signal transducers accompany the germline lesion. In HAVCR2 p.Tyr82Cys
    tumours the transcriptional program is enriched for IL6-JAK-STAT3 and for
    TNF signalling via NF-kappaB, which is the stated rationale for JAK
    inhibition.
  cell_types:
  - preferred_term: CD8-positive, alpha-beta cytotoxic T cell
    term:
      id: CL:0000794
      label: CD8-positive, alpha-beta cytotoxic T cell
  biological_processes:
  - preferred_term: cell surface receptor signaling pathway via JAK-STAT
    modifier: INCREASED
    term:
      id: GO:0007259
      label: cell surface receptor signaling pathway via JAK-STAT
  - preferred_term: canonical NF-kappaB signal transduction
    modifier: INCREASED
    term:
      id: GO:0007249
      label: canonical NF-kappaB signal transduction
  locations:
  - preferred_term: subcutaneous adipose tissue
    term:
      id: UBERON:0002190
      label: subcutaneous adipose tissue
  evidence:
  - reference: PMID:17934071
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: definition, classification, and prognostic factors: an EORTC Cutaneous Lymphoma Group Study of 83 cases."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "SPTL-ABs were generally confined to the subcutis, had a CD4-, CD8+, CD56-, betaF1+ phenotype, were uncommonly associated with a hemophagocytic syndrome (HPS; 17%), and had a favorable prognosis (5-year overall survival [OS]: 82%)."
    explanation: >-
      Defines the immunophenotype and the subcutaneous localisation of the
      expanding clone.
  - reference: PMID:34535012
    reference_title: "Genetic profiles of subcutaneous panniculitis-like T-cell lymphoma and clinicopathological impact of HAVCR2 mutations."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "At the gene expression level, HAVCR2Y82C SPTCLs were enriched in genes involved in IL6-JAK-STAT3 signaling and in tumor necrosis factor-α signaling via NF-κB."
    explanation: >-
      Transcriptomic evidence for the two signalling programs annotated on this
      node.
  - reference: PMID:30792187
    reference_title: "Frequent germline mutations of HAVCR2 in sporadic subcutaneous panniculitis-like T-cell lymphoma."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "SPTCL cells also harbored somatic mutations (6.2 per patient) that are frequently identified in genes associated with epigenetic regulation and signal transduction."
    explanation: >-
      Establishes the cooperating somatic mutation burden in the neoplastic
      clone.
  downstream:
  - target: Adipocyte Rimming and Lobular Panniculitis
    description: >-
      The expanded cytotoxic clone encircles and kills individual adipocytes
      within the fat lobule.
- name: Adipocyte Rimming and Lobular Panniculitis
  biological_scale: TISSUE
  description: >-
    The histologic hallmark of the disease: atypical cytotoxic lymphocytes
    surround individual adipocytes in a lace-like pattern within a lobular
    panniculitis, with karyorrhexis and fat necrosis and without epidermal
    involvement. Adipocyte death is the direct tissue-level readout of
    T-cell-mediated cytotoxicity in this compartment.
  cell_types:
  - preferred_term: adipocyte
    term:
      id: CL:0000136
      label: adipocyte
  - preferred_term: CD8-positive, alpha-beta cytotoxic T cell
    term:
      id: CL:0000794
      label: CD8-positive, alpha-beta cytotoxic T cell
  biological_processes:
  - preferred_term: T cell mediated cytotoxicity
    modifier: INCREASED
    term:
      id: GO:0001913
      label: T cell mediated cytotoxicity
  - preferred_term: apoptotic process
    modifier: INCREASED
    term:
      id: GO:0006915
      label: apoptotic process
  locations:
  - preferred_term: subcutaneous adipose tissue
    term:
      id: UBERON:0002190
      label: subcutaneous adipose tissue
  evidence:
  - reference: PMID:34535012
    reference_title: "Genetic profiles of subcutaneous panniculitis-like T-cell lymphoma and clinicopathological impact of HAVCR2 mutations."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Histopathologically, SPTCL is characterized by CD8-positive T cells infiltrating into subcutaneous adipose tissue, with rimmed individual fat cells in a lace-like pattern."
    explanation: >-
      States the rimming pattern and the tissue compartment this node
      describes.
  - reference: PMID:30126736
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: Clinical features, therapeutic approach, and outcome in a case series of 16 patients."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Histopathology typically showed a lobular panniculitis with individual adipocytes surrounded by atypical lymphocytes, usually with a CD3+, CD4-, CD8+, CD56-, TIA1 cytotoxic granule associated RNA binding protein 1-positive phenotype and high proliferation rate."
    explanation: >-
      Independent confirmation of the lobular panniculitis pattern and the
      cytotoxic phenotype of the rimming cells.
  downstream:
  - target: Subcutaneous Nodules and Plaques
    description: >-
      Destructive lobular panniculitis is what the patient feels and the
      clinician sees as nodules and plaques.
- name: Macrophage Hyperactivation and Hemophagocytosis
  biological_scale: ORGANISM
  description: >-
    In a substantial minority of patients the innate activation described above
    escalates into full hemophagocytic lymphohistiocytosis, with activated
    macrophages engulfing blood cells in marrow, spleen and liver and a
    systemic cytokine excess producing fever, cytopenias, hyperferritinaemia,
    hypertriglyceridaemia and hypofibrinogenaemia. HLH risk tracks HAVCR2
    genotype dose and is higher in children and in males.
  cell_types:
  - preferred_term: macrophage
    term:
      id: CL:0000235
      label: macrophage
  biological_processes:
  - preferred_term: macrophage activation
    modifier: INCREASED
    term:
      id: GO:0042116
      label: macrophage activation
  - preferred_term: inflammatory response
    modifier: INCREASED
    term:
      id: GO:0006954
      label: inflammatory response
  evidence:
  - reference: PMID:34535012
    reference_title: "Genetic profiles of subcutaneous panniculitis-like T-cell lymphoma and clinicopathological impact of HAVCR2 mutations."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "HAVCR2Y82C was associated with younger age (P = .001), development of hemophagocytic lymphohistiocytosis or hemophagocytic lymphohistiocytosis-like systemic illness (P < .001), and short relapse-free survival (RFS) (P = .023)."
    explanation: >-
      Links the germline genotype to the HLH endpoint in a nationwide cohort.
  - reference: PMID:37051767
    reference_title: "Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Homozygous HAVCR2Y82C mutation was more common in the presence of HLH compared with the absence (75.0% vs. 44.4%; P=0.02)."
    explanation: >-
      Shows the genotype dose effect on HLH occurrence within an SPTCL cohort.
  downstream:
  - target: Hemophagocytic Lymphohistiocytosis
    description: >-
      Systemic macrophage activation is the mechanism behind the clinical HLH
      syndrome.
phenotypes:
- category: Integument
  name: Subcutaneous Nodules and Plaques
  description: >-
    Multiple, usually painless subcutaneous nodules and plaques, preferentially
    on the legs and trunk. They are the presenting complaint in nearly all
    patients and are routinely mistaken for a benign panniculitis, cellulitis
    or erythema nodosum, which is the main source of diagnostic delay.
  phenotype_term:
    preferred_term: Subcutaneous nodule
    term:
      id: HP:0001482
      label: Subcutaneous nodule
  frequency: VERY_FREQUENT
  diagnostic: true
  evidence:
  - reference: PMID:30126736
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: Clinical features, therapeutic approach, and outcome in a case series of 16 patients."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Patients presented with multiple nodular or plaque-like lesions preferentially affecting the legs and/or trunk."
    explanation: >-
      Describes the lesion morphology and distribution recorded here.
  - reference: PMID:35509196
    reference_title: "The pathophysiology and current treatments for the subcutaneous panniculitis-like T cell lymphoma: An updated review."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "SPTCL is usually presented clinically as painless subcutaneous and erythematous nodules over the trunk or extremities."
    explanation: >-
      Confirms that the nodules are characteristically painless, which is part
      of why they are initially dismissed.
- category: Integument
  name: Lobular Panniculitis
  description: >-
    Inflammation of the subcutaneous fat lobule, which is simultaneously the
    clinical presentation and the histologic substrate of the disease. In some
    HAVCR2-mutant paediatric patients the biopsy shows panniculitis without
    sufficient evidence of lymphoma.
  phenotype_term:
    preferred_term: Panniculitis
    term:
      id: HP:0012490
      label: Panniculitis
  frequency: VERY_FREQUENT
  evidence:
  - reference: PMID:37062931
    reference_title: "Efficacy of ruxolitinib for HAVCR2 mutation-associated hemophagocytic lymphohistiocytosis and panniculitis manifestations in children."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Histopathologically, only two patients were diagnosed with SPTCL and three were reported as panniculitis with no sufficient evidence of lymphoma."
    explanation: >-
      Documents panniculitis as the histologic finding, including cases where
      it falls short of a lymphoma diagnosis.
- category: Neoplasm
  name: Hemophagocytic Lymphohistiocytosis
  description: >-
    A systemic hyperinflammatory syndrome complicating a substantial minority
    of cases, defined by the HLH-2004 criteria. It is the dominant adverse
    prognostic factor and the main cause of disease-related death. Reported
    frequency varies widely with the population studied - about 17% in the
    adult-weighted EORTC series, about two thirds in a paediatric cohort
    selected for HAVCR2 sequencing.
  phenotype_term:
    preferred_term: Hemophagocytosis
    term:
      id: HP:0012156
      label: Hemophagocytosis
  frequency: OCCASIONAL
  evidence:
  - reference: PMID:17934071
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: definition, classification, and prognostic factors: an EORTC Cutaneous Lymphoma Group Study of 83 cases."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "SPTL-ABs were generally confined to the subcutis, had a CD4-, CD8+, CD56-, betaF1+ phenotype, were uncommonly associated with a hemophagocytic syndrome (HPS; 17%), and had a favorable prognosis (5-year overall survival [OS]: 82%)."
    explanation: >-
      Gives the 17% frequency underpinning the OCCASIONAL band for unselected
      alpha/beta SPTCL.
  - reference: PMID:39538229
    reference_title: "Characteristics and therapeutic outcomes of subcutaneous panniculitis-like T-cell lymphoma with and without germline HAVCR2 mutations in Thai children and adolescents."
    supports: SUPPORT
    directness: DIRECT
    evidence_source: HUMAN_CLINICAL
    snippet: "86.4% harbored germline HAVCR2 mutation, either homozygous (77.3%) or heterozygous (9.1%) p.Y82C variant, while 68.2% developed HLH/HLH-like systemic illnesses."
    explanation: >-
      Shows that in a paediatric, HAVCR2-enriched cohort HLH is the majority
      outcome, so the frequency band is population-dependent.
- category: Constitutional
  name: Fever
  description: >-
    Constitutional fever, generally in the context of HLH or HLH-like systemic
    illness rather than uncomplicated cutaneous disease.
  phenotype_term:
    preferred_term: Fever
    term:
      id: HP:0001945
      label: Fever
  evidence:
  - reference: PMID:37051767
    reference_title: "Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Those incompletely fulfilling the criteria but being clinically consistent with HLH (i.e., fever, cytopenias, serum ferritin ≥500 μg/L, and the presence of hemophagocytosis in BM) were accounted for ‘HLH-like systemic illnesses’."
    explanation: >-
      Names fever as a defining feature of the HLH-like systemic illness seen
      in these patients.
- category: Blood
  name: Cytopenias
  description: >-
    Peripheral cytopenias affecting two or more lineages are part of the HLH
    definition applied in these cohorts and accompany the systemic phase of
    disease.
  phenotype_term:
    preferred_term: Thrombocytopenia
    term:
      id: HP:0001873
      label: Thrombocytopenia
  evidence:
  - reference: PMID:37051767
    reference_title: "Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "in clinical practice, patients with high-grade fever, cytopenias and presence of hemophagocytic activity in bone marrow (BM) can be presumptively diagnosed as having hemophagocytic syndrome (HPS)."
    explanation: >-
      Records cytopenias as a core clinical feature of the hemophagocytic
      phase.
- category: Blood
  name: Hyperferritinemia
  description: >-
    Marked elevation of serum ferritin, used both as an HLH-2004 criterion and
    as a practical surveillance marker in patients with known HAVCR2 variants.
  phenotype_term:
    preferred_term: Increased circulating ferritin concentration
    term:
      id: HP:0003281
      label: Increased circulating ferritin concentration
  evidence:
  - reference: PMID:37051767
    reference_title: "Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Those incompletely fulfilling the criteria but being clinically consistent with HLH (i.e., fever, cytopenias, serum ferritin ≥500 μg/L, and the presence of hemophagocytosis in BM) were accounted for ‘HLH-like systemic illnesses’."
    explanation: >-
      Gives the explicit ferritin threshold used to define HLH-like systemic
      illness in this disease.
genetic:
- name: HAVCR2
  gene_term:
    preferred_term: HAVCR2
    term:
      id: hgnc:18437
      label: HAVCR2
  relationship_type: SUSCEPTIBILITY
  variant_origin: GERMLINE
  frequency: >-
    Reported in roughly 50% to 86% of patients depending on cohort ancestry and
    on whether the series is enriched for paediatric or HLH-complicated
    disease.
  notes: >-
    HAVCR2 encodes TIM-3, an inhibitory checkpoint receptor on T cells and
    innate immune cells. Germline loss-of-function missense alleles are the
    only recurrent genetic lesion established in SPTCL. Three recurrent
    substitutions are reported - p.Tyr82Cys, p.Ile97Met and p.Thr101Ile - all
    in the extracellular immunoglobulin variable-like domain.
  case_fractions:
  - population: Korean nationwide SPTCL cohort
    case_fraction_percent: 51.0
    cohort_size: 49
    notes: >-
      Numerator is p.Tyr82Cys specifically. That is comparable with the Thai
      row, where every mutation detected was also p.Y82C, but not with the
      integrated-reanalysis row, which counts any germline HAVCR2 mutation.
    evidence:
    - reference: PMID:34535012
      reference_title: "Genetic profiles of subcutaneous panniculitis-like T-cell lymphoma and clinicopathological impact of HAVCR2 mutations."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "Of 49 patients with available HAVCR2 status, 25 (51.0%) were HAVCR2Y82C."
      explanation: >-
        Quantifies the p.Tyr82Cys share in an unselected Korean national
        cohort.
  - population: Integrated series of six Japanese patients plus 30 reanalysed public exomes
    case_fraction_percent: 79.3
    cohort_size: 29
    notes: >-
      Any germline HAVCR2 mutation, in 23 of the 29 patients with an evaluable
      genotype. This is not an independent cohort and should not be counted as
      one: only six patients are the authors' own series, and the other 30 are
      public exome data whose SPTCL content overlaps the discovery cohorts
      already cited in this block. It is recorded because the reanalysis is a
      separate observation of the same axis, not because it adds 29 new
      patients.
    evidence:
    - reference: PMID:39288772
      reference_title: "Genetic profiles and clinical features in subcutaneous panniculitis-like T-cell lymphomas."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "We identified 138 somatic mutations in skin tumors of 24 patients and HAVCR2 germline mutations in 23 of 29 patients."
      explanation: >-
        Gives the carrier fraction recorded here.
    - reference: PMID:39288772
      reference_title: "Genetic profiles and clinical features in subcutaneous panniculitis-like T-cell lymphomas."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "we integrated whole-exome sequencing data from 60 samples collected from 36 SPTCL patients, encompassing six patients of our cohort and 30 patients of publicly available data."
      explanation: >-
        Establishes the composition of the series, which is why this row is
        labelled as an integrated reanalysis rather than as an independent
        cohort.
    - reference: PMID:39288772
      reference_title: "Genetic profiles and clinical features in subcutaneous panniculitis-like T-cell lymphomas."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "HAVCR2 p.Tyr82Cys mutations were identified in four of six Japanese patients."
      explanation: >-
        Records the p.Tyr82Cys share in the study's own Japanese arm, which is
        n=6 and correspondingly fragile.
  - population: Thai SPTCL cohort aged 20 years or younger
    case_fraction_percent: 86.4
    cohort_size: 22
    notes: >-
      Numerator is any germline HAVCR2 mutation across the 22 patients aged 20
      years or younger enrolled from six Thai centres. In this cohort the two
      are the same set: every mutation detected was p.Y82C, homozygous in 77.3%
      and heterozygous in 9.1%, which sums to the 86.4%. So this row is
      comparable with the Korean p.Tyr82Cys row on numerator, and differs from
      it on ascertainment - paediatric rather than unselected - which is the
      likelier source of the gap between 51% and 86.4%.
    evidence:
    - reference: PMID:39538229
      reference_title: "Characteristics and therapeutic outcomes of subcutaneous panniculitis-like T-cell lymphoma with and without germline HAVCR2 mutations in Thai children and adolescents."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "86.4% harbored germline HAVCR2 mutation, either homozygous (77.3%) or heterozygous (9.1%) p.Y82C variant, while 68.2% developed HLH/HLH-like systemic illnesses."
      explanation: >-
        Gives the much higher carrier fraction in a paediatric series, showing
        the ascertainment dependence of this number.
    - reference: PMID:39538229
      reference_title: "Characteristics and therapeutic outcomes of subcutaneous panniculitis-like T-cell lymphoma with and without germline HAVCR2 mutations in Thai children and adolescents."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "Fifth, only HAVCR2 p.Y82C variant was identified in our study population of exclusively Thai pediatric patients with SPTCL."
      explanation: >-
        Confirms that every mutation detected in this cohort was p.Y82C, which
        is what makes its 86.4% comparable on numerator with the Korean
        p.Tyr82Cys row.
    - reference: PMID:39538229
      reference_title: "Characteristics and therapeutic outcomes of subcutaneous panniculitis-like T-cell lymphoma with and without germline HAVCR2 mutations in Thai children and adolescents."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "Based on the Genome Aggregation Database (gnomAD), although HAVCR2 p.Y82C mutation in the general population is rare with a minor allele frequency (MAF) of 3.6 x 10-3, its ethnicity-specific MAFs are variable, ranging from 4.2 x 10-5 in Africans to 2.1 x 10-2 in East Asians"
      explanation: >-
        Evidences the ascertainment reading rather than leaving it asserted. The
        same paper puts the Southeast Asian allele frequency an order of
        magnitude below the East Asian one, yet this Southeast Asian cohort has
        the higher carrier fraction of the two - so ancestry does not account
        for the gap, and paediatric ascertainment is the remaining explanation.
  evidence:
  - reference: PMID:30792187
    reference_title: "Frequent germline mutations of HAVCR2 in sporadic subcutaneous panniculitis-like T-cell lymphoma."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Consistent with a recent report, germline mutations in HAVCR2, encoding T-cell immunoglobulin mucin 3 (TIM3), were identified in 11 of 13 (85%) cases."
    explanation: >-
      Independent replication of the HAVCR2 association in an Asian cohort.
  variants:
  - name: HAVCR2 c.245A>G p.Tyr82Cys
    description: >-
      The commonest reported allele, carried on a probable founder chromosome
      in patients of East Asian and Polynesian ancestry. Causes TIM-3
      misfolding and loss of plasma membrane expression.
    gene:
      preferred_term: HAVCR2
      term:
        id: hgnc:18437
        label: HAVCR2
    clinical_significance: PATHOGENIC
    evidence:
    - reference: PMID:30374066
      reference_title: "Germline HAVCR2 mutations altering TIM-3 characterize subcutaneous panniculitis-like T cell lymphomas with hemophagocytic lymphohistiocytic syndrome."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "The variant encoding p.Tyr82Cys TIM-3 occurs on a potential founder chromosome in patients with East Asian and Polynesian ancestry, while p.Ile97Met TIM-3 occurs in patients with European ancestry."
      explanation: >-
        Establishes the founder origin and ancestry distribution of this
        allele.
  - name: HAVCR2 c.291A>G p.Ile97Met
    description: >-
      The predominant allele in patients of European ancestry, with the same
      misfolding and trafficking defect as p.Tyr82Cys.
    gene:
      preferred_term: HAVCR2
      term:
        id: hgnc:18437
        label: HAVCR2
    clinical_significance: PATHOGENIC
    evidence:
    - reference: PMID:30374066
      reference_title: "Germline HAVCR2 mutations altering TIM-3 characterize subcutaneous panniculitis-like T cell lymphomas with hemophagocytic lymphohistiocytic syndrome."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "We identify in ~60% of SPTCL cases germline, loss-of-function, missense variants altering highly conserved residues of TIM-3, c.245A>G (p.Tyr82Cys) and c.291A>G (p.Ile97Met), each with specific geographic distribution."
      explanation: >-
        Names the coding change and its loss-of-function classification.
  - name: HAVCR2 p.Thr101Ile
    description: >-
      A third recurrent allele, reported in compound heterozygosity with
      p.Tyr82Cys.
    gene:
      preferred_term: HAVCR2
      term:
        id: hgnc:18437
        label: HAVCR2
    clinical_significance: LIKELY_PATHOGENIC
    evidence:
    - reference: PMID:30792187
      reference_title: "Frequent germline mutations of HAVCR2 in sporadic subcutaneous panniculitis-like T-cell lymphoma."
      supports: SUPPORT
      evidence_source: HUMAN_CLINICAL
      snippet: "Ten patients harbored homozygous p.Y82C mutations, and 1 showed compound heterozygous mutations (p.Y82C and p.T101I)."
      explanation: >-
        Documents p.Thr101Ile as the second allele in a compound heterozygous
        patient.
histopathology:
- name: Adipocyte rimming by atypical lymphoid cells
  description: >-
    Atypical lymphoid cells encircling individual adipocytes within the
    subcutaneous fat lobule. This is the defining diagnostic finding and is
    assessed on a deep incisional or excisional biopsy rather than a
    superficial punch.
  diagnostic: true
  evidence:
  - reference: PMID:37051767
    reference_title: "Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The pathological hallmark of SPTCL is an adipocyte rimming by atypical lymphoid cells expressing CD3, CD8, T-cell intracytoplasmic antigen 1 (TIA-1) and T-cell receptor β F1 (BF1)."
    explanation: >-
      States the hallmark finding and the accompanying immunophenotype.
- name: Ki-67 hotspots among rimming CD8-positive T cells
  description: >-
    Foci of high proliferative activity within the CD8-positive rimming
    infiltrate. Their presence separates SPTCL from lupus erythematosus
    panniculitis on a four-stain panel, and their absence argues against
    lymphoma.
  diagnostic: true
  evidence:
  - reference: PMID:26796503
    reference_title: "Useful Parameters for Distinguishing Subcutaneous Panniculitis-like T-Cell Lymphoma From Lupus Erythematosus Panniculitis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Ki-67 hotspots were not identified in LEP, thus aiding the distinction of SPTCL from LEP."
    explanation: >-
      Establishes the discriminatory value of the finding against the principal
      histologic mimic.
diagnosis:
- name: Deep skin biopsy with immunophenotyping
  description: >-
    Diagnosis rests on a deep biopsy showing lobular panniculitis with adipocyte
    rimming, plus an immunohistochemical panel establishing the CD3-positive,
    CD4-negative, CD8-positive, CD56-negative, betaF1-positive cytotoxic
    phenotype. Demonstrating a clonal T-cell receptor rearrangement supports the
    diagnosis.
  evidence:
  - reference: PMID:30126736
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: Clinical features, therapeutic approach, and outcome in a case series of 16 patients."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Histopathology typically showed a lobular panniculitis with individual adipocytes surrounded by atypical lymphocytes, usually with a CD3+, CD4-, CD8+, CD56-, TIA1 cytotoxic granule associated RNA binding protein 1-positive phenotype and high proliferation rate."
    explanation: >-
      Sets out the histologic and immunophenotypic criteria used in practice.
- name: Germline HAVCR2 sequencing
  description: >-
    Sequencing of HAVCR2 exon 2 covers the three recurrent alleles and is
    increasingly performed at diagnosis, particularly in children and in
    patients with HLH, because a positive result changes surveillance, family
    counselling and - if transplantation is considered - donor selection.
    Reduced TIM-3 surface expression by flow cytometry has been proposed as a
    screening test.
  evidence:
  - reference: PMID:37051767
    reference_title: "Germline HAVCR2 mutations and their relation to the clinical spectrum of subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis: results from a multicenter study and meta-analysis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The designed primer could cover pathogenic HAVCR2 variants of p.Y82C, p.I97M and p.T101I."
    explanation: >-
      Confirms that exon 2 sequencing captures all three recurrent alleles.
  - reference: PMID:32285995
    reference_title: "TIM-3 deficiency presenting with two clonally unrelated episodes of mesenteric and subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "We show that mesenteric fatty tissue localization of SPTCL can be the presenting manifestation of TIM-3 deficiency, that this condition predisposes to recurrent lymphoma, and that flow cytometry is a possible screening tool."
    explanation: >-
      Supports flow cytometry as a screening approach and documents the
      recurrence risk that motivates genotyping.
- name: FDG PET/CT for staging and response assessment
  description: >-
    Used to define the extent of subcutaneous disease, look for extracutaneous
    involvement and follow treatment response.
  evidence:
  - reference: PMID:35509196
    reference_title: "The pathophysiology and current treatments for the subcutaneous panniculitis-like T cell lymphoma: An updated review."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Positron emission tomography scan is utilized for disease staging and treatment follow-up."
    explanation: >-
      States the role of PET in staging and follow-up for this disease.
differential_diagnoses:
- name: Lupus erythematosus panniculitis
  description: >-
    The principal histologic mimic. The two overlap clinically and
    histologically and can coexist in the same patient, but SPTCL carries the
    risk of HLH and so the distinction matters. Molecular profiling separates
    them, and overlapping cases cluster with lupus panniculitis rather than
    with SPTCL.
  distinguishing_features:
  - Ki-67 hotspots enriched in atypical CD8-positive T cells are present in SPTCL and absent in lupus panniculitis
  - Clonal T-cell receptor rearrangement favours SPTCL
  - Gene expression profiling separates the two entities, with overlap cases resembling lupus panniculitis
  evidence:
  - reference: PMID:26796503
    reference_title: "Useful Parameters for Distinguishing Subcutaneous Panniculitis-like T-Cell Lymphoma From Lupus Erythematosus Panniculitis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Lymphocyte atypia combined with adipocyte rimming of CD8+ T cells within Ki-67 hotspots was also highly specific for the diagnosis of SPTCL."
    explanation: >-
      Provides the specific histologic combination that discriminates the two.
  - reference: PMID:33966586
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma, lupus erythematosus profundus, and overlapping cases: molecular characterization through the study of 208 genes."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Gene expression unsupervised analysis of the samples differentiated SPTCL from LEP samples. Most overlapping cases were clustered with LEP cases."
    explanation: >-
      Molecular evidence that the entities are separable and that overlap cases
      behave like lupus panniculitis.
- name: Primary cutaneous gamma-delta T-cell lymphoma
  description: >-
    Formerly grouped with SPTCL under a single label. It carries a gamma/delta
    rather than alpha/beta receptor, frequently involves the epidermis and
    ulcerates, and has a far worse outcome irrespective of treatment. Separating
    the two on betaF1 and TCR-delta staining is the reason the term SPTCL is now
    restricted to the alpha/beta entity.
  distinguishing_features:
  - CD4-negative, CD8-negative, CD56 variable, betaF1-negative phenotype
  - Frequent epidermal or dermal involvement and ulceration rather than disease confined to the subcutis
  - 5-year overall survival of 11% versus 82% for the alpha/beta entity
  evidence:
  - reference: PMID:17934071
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: definition, classification, and prognostic factors: an EORTC Cutaneous Lymphoma Group Study of 83 cases."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "SPTL-GDs often showed (epi)dermal involvement and/or ulceration, a CD4-, CD8-, CD56+/-, betaF1- T-cell phenotype, and poor prognosis (5-year OS: 11%), irrespective of the presence of HPS or type of treatment."
    explanation: >-
      Gives the phenotype, distribution and outcome that separate the
      gamma/delta entity.
  - reference: PMID:17934071
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: definition, classification, and prognostic factors: an EORTC Cutaneous Lymphoma Group Study of 83 cases."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "These results indicate that SPTL-AB and SPTL-GD are distinct entities, and justify that the term SPTL should further be used only for SPTL-AB."
    explanation: >-
      The nomenclature decision that makes this a differential rather than a
      subtype.
treatments:
- name: Corticosteroid-based Immunosuppressive Therapy
  description: >-
    Systemic corticosteroids alone or combined with low-dose methotrexate or
    cyclosporine A. This is now the usual first-line choice for uncomplicated
    cutaneous disease, and gives high complete response rates without the
    toxicity of anthracycline-based chemotherapy. Corticosteroid monotherapy
    relapses more often than corticosteroids combined with another
    immunoregulatory agent.
  therapeutic_modality: SMALL_MOLECULE
  treatment_term:
    preferred_term: Pharmacotherapy
    term:
      id: NCIT:C15986
      label: Pharmacotherapy
    therapeutic_agent:
    - preferred_term: prednisone
      term:
        id: CHEBI:8382
        label: prednisone
    - preferred_term: methotrexate
      term:
        id: CHEBI:44185
        label: methotrexate
    - preferred_term: cyclosporin A
      term:
        id: CHEBI:4031
        label: cyclosporin A
  target_mechanisms:
  - target: Unrestrained Innate Immune Activation
    description: >-
      Broad suppression of cytokine production and lymphocyte activation, which
      is why an immunosuppressive rather than cytotoxic strategy works in a
      disease driven by loss of an inhibitory checkpoint.
  evidence:
  - reference: PMID:30126736
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma: Clinical features, therapeutic approach, and outcome in a case series of 16 patients."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Oral steroids alone or in combination with low-dose methotrexate or cyclosporine A were the most common initial treatment, achieving a complete response in 85% of the treated patients."
    explanation: >-
      Gives the regimen and the complete response rate recorded here.
  - reference: PMID:37840116
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma associated with hemophagocytic lymphohistiocytosis: a systematic review of 63 patients reported in the literature."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The corticosteroid monotherapy experienced a higher recurrence rate than the corticosteroids plus other immunoregulatory agents therapy (66.7 vs. 0.0%, p = 0.029)."
    explanation: >-
      Supports combining corticosteroids with a second immunoregulatory agent
      rather than using steroids alone.
- name: Multiagent Chemotherapy
  description: >-
    Anthracycline-based combination chemotherapy, historically the default and
    now reserved for patients presenting with HLH or progressing on
    immunosuppression. In a paediatric comparison it achieved a numerically
    higher durable complete remission rate than immunosuppressive therapy but at
    the cost of more adverse events, and the difference in remission rate was
    not significant.
  therapeutic_modality: SMALL_MOLECULE
  treatment_term:
    preferred_term: chemotherapy
    term:
      id: NCIT:C15632
      label: Chemotherapy
  evidence:
  - reference: PMID:39538229
    reference_title: "Characteristics and therapeutic outcomes of subcutaneous panniculitis-like T-cell lymphoma with and without germline HAVCR2 mutations in Thai children and adolescents."
    supports: SUPPORT
    directness: DIRECT
    evidence_source: HUMAN_CLINICAL
    snippet: "Durable complete remission (CR) was achieved in 71.4% and 50.0% after first-line chemotherapy and IST, respectively (P=0.45); however, chemotherapy tended to increase any AEs compared to IST (57.1% vs. 12.5%; P=0.07)."
    explanation: >-
      Reports the efficacy and toxicity trade-off between chemotherapy and
      immunosuppression without establishing superiority of either.
  - reference: PMID:15368328
    reference_title: "Immunophenotypic and molecular features, clinical outcomes, treatments, and prognostic factors associated with subcutaneous panniculitis-like T-cell lymphoma: a systematic analysis of 156 patients reported in the literature."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Anthracycline-based chemotherapy regimens were the most commonly used and most effective systemic treatment options, producing long-term CR in approximately 30% of patients."
    explanation: >-
      Documents the historical role and the durable remission rate of
      anthracycline-based regimens.
- name: Ruxolitinib
  description: >-
    A JAK1/JAK2 inhibitor. Its use follows directly from the mechanism: TIM-3
    loss drives cytokine-mediated inflammation and HAVCR2-mutant tumours are
    transcriptionally enriched for IL6-JAK-STAT3 signalling. Reported responses
    in HAVCR2-mutant children have been rapid and durable after corticosteroids,
    other immunosuppressants and chemotherapy had all failed.
  therapeutic_modality: SMALL_MOLECULE
  treatment_term:
    preferred_term: Pharmacotherapy
    term:
      id: NCIT:C15986
      label: Pharmacotherapy
    therapeutic_agent:
    - preferred_term: ruxolitinib
      term:
        id: CHEBI:66919
        label: ruxolitinib
  target_mechanisms:
  - target: Clonal Cytotoxic Alpha-Beta T-cell Expansion
    description: >-
      Blocks the JAK-STAT signalling program enriched in HAVCR2 p.Tyr82Cys
      tumours.
  - target: Macrophage Hyperactivation and Hemophagocytosis
    description: >-
      Suppresses the cytokine signalling that sustains the hemophagocytic
      syndrome.
  evidence:
  - reference: PMID:37062931
    reference_title: "Efficacy of ruxolitinib for HAVCR2 mutation-associated hemophagocytic lymphohistiocytosis and panniculitis manifestations in children."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "All patients initially received corticosteroids, immunosuppressants or chemotherapy, achieving unfavourable responses. Strikingly, they responded well to ruxolitinib targeting inflammatory cytokines, allowing rapid disease resolution and/or long-term maintenance of remission."
    explanation: >-
      Reports responses to ruxolitinib after failure of conventional therapy in
      genotyped patients.
  - reference: PMID:32271897
    reference_title: "Efficacy of ruxolitinib in subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "First evidence of ruxolitinib efficacy for subcutaneous panniculitis-like T-cell lymphoma with hemophagocytic lymphohistiocytosis."
    explanation: >-
      The first report of ruxolitinib activity in this indication.
- name: Hematopoietic Stem Cell Transplantation
  description: >-
    Reserved for refractory or relapsed disease, particularly HLH-complicated
    disease. Because the predisposing HAVCR2 variant is germline, donor genotype
    matters: a relapse has been reported after a sibling-identical transplant
    from a donor who turned out to carry the same homozygous HAVCR2 mutation.
  therapeutic_modality: CELL_THERAPY
  treatment_term:
    preferred_term: Hematopoietic Cell Transplantation
    term:
      id: NCIT:C15431
      label: Hematopoietic Cell Transplantation
  evidence:
  - reference: PMID:37840116
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma associated with hemophagocytic lymphohistiocytosis: a systematic review of 63 patients reported in the literature."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Fifteen patients, including 5 with relapsed/refractory SPTCL-HLH, responded well and survived after receiving SCT."
    explanation: >-
      Supports transplantation as an effective option in refractory disease.
  - reference: PMID:37840116
    reference_title: "Subcutaneous panniculitis-like T-cell lymphoma associated with hemophagocytic lymphohistiocytosis: a systematic review of 63 patients reported in the literature."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "One case who received a sibling-identical SCT relapsed. Further analysis revealed a homozygous HAVCR2 mutation with the donor."
    explanation: >-
      Documents the germline-genotype pitfall in related-donor selection.
- name: Radiation Therapy
  description: >-
    Skin-directed radiotherapy for localised or solitary lesions, avoiding
    systemic exposure in patients whose disease is anatomically limited.
  therapeutic_modality: RADIOTHERAPY
  treatment_term:
    preferred_term: Radiation Therapy
    term:
      id: NCIT:C15313
      label: Radiation Therapy
  evidence:
  - reference: PMID:15368328
    reference_title: "Immunophenotypic and molecular features, clinical outcomes, treatments, and prognostic factors associated with subcutaneous panniculitis-like T-cell lymphoma: a systematic analysis of 156 patients reported in the literature."
    supports: SUPPORT
    directness: INDIRECT
    evidence_source: HUMAN_CLINICAL
    snippet: "The authors performed a systematic analysis of all patients with SPTCL reported on in the English-language medical literature, with emphasis on specific clinical features, experiences involving the use of radiotherapy and systemic agents, and prognostic factors predictive of treatment response and clinical outcome."
    explanation: >-
      Establishes that radiotherapy is part of the reported treatment
      repertoire; this pooled review does not isolate its efficacy.
discussions:
- discussion_id: sptcl_neoplastic_vs_inflammatory
  kind: KNOWLEDGE_GAP
  status: OPEN
  prompt: >-
    Is HAVCR2-mutant subcutaneous panniculitis-like T-cell lymphoma a lymphoma,
    or an inherited autoinflammatory disease that produces a clonal
    lymphocytic infiltrate?
  attaches_to:
  - pathophysiology#Clonal Cytotoxic Alpha-Beta T-cell Expansion
  rationale: >-
    Several observations sit uneasily with a neoplastic model. Immunosuppression
    outperforms cytotoxic chemotherapy; JAK inhibition produces rapid remission
    in genotyped patients who failed chemotherapy; some HAVCR2-mutant children
    have panniculitis without histologic evidence of lymphoma at all; and a
    patient has been described with two clonally unrelated episodes, which is
    hard to reconcile with a single transformed clone. The authors of two of
    these reports say the neoplastic nature of the condition is in question. The
    KB models this as a lymphoma entry because that is its classification and
    because clonal T-cell receptor rearrangement is a diagnostic criterion, but
    the mechanism nodes here deliberately place the germline immune lesion
    upstream of the clone rather than the reverse.
  evidence:
  - reference: PMID:32271897
    reference_title: "Efficacy of ruxolitinib in subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Supporting rationale for ruxolitinib use, not more aggressive treatment, in this context, questioning this condition’s neoplastic nature."
    explanation: >-
      States the question explicitly on the basis of the treatment response.
  - reference: PMID:37062931
    reference_title: "Efficacy of ruxolitinib for HAVCR2 mutation-associated hemophagocytic lymphohistiocytosis and panniculitis manifestations in children."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "The excellent efficacy of ruxolitinib highlights this disease as an inflammatory condition instead of neoplastic nature and indicates novel agents targeting key inflammatory pathways as an encouraging approach for this disease entity."
    explanation: >-
      An independent group drawing the same inference from the ruxolitinib
      response.
  - reference: PMID:32285995
    reference_title: "TIM-3 deficiency presenting with two clonally unrelated episodes of mesenteric and subcutaneous panniculitis-like T-cell lymphoma and hemophagocytic lymphohistiocytosis."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "We show that mesenteric fatty tissue localization of SPTCL can be the presenting manifestation of TIM-3 deficiency, that this condition predisposes to recurrent lymphoma, and that flow cytometry is a possible screening tool."
    explanation: >-
      Two clonally unrelated episodes in one patient argue for a predisposing
      immune defect rather than a single transformed clone.
- discussion_id: sptcl_havcr2_wildtype_mechanism
  kind: KNOWLEDGE_GAP
  status: OPEN
  prompt: >-
    What drives the HAVCR2 wild-type cases, which are roughly half of an
    unselected cohort?
  attaches_to:
  - pathophysiology#Germline TIM-3 Loss of Function
  rationale: >-
    The mechanism recorded in this entry starts from germline HAVCR2 loss of
    function, but about half of patients in an unselected national cohort have
    no HAVCR2 variant. Mutations in UNC13D, PIAS3 and KMT2D are reported more
    often in those cases, and CCR4 is upregulated in them, but no unifying
    mechanism has been established. The entry therefore has no upstream node
    for the wild-type group.
  evidence:
  - reference: PMID:34535012
    reference_title: "Genetic profiles of subcutaneous panniculitis-like T-cell lymphoma and clinicopathological impact of HAVCR2 mutations."
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Mutations in UNC13D, PIAS3, and KMT2D were more frequent in HAVCR2WT SPTCLs."
    explanation: >-
      Names the candidate lesions that distinguish the wild-type group without
      establishing a mechanism for it.
notes: >-
  Entity scope: this entry covers the alpha/beta phenotype only, following the
  2008 EORTC decision to restrict the term SPTCL to that entity. Primary
  cutaneous gamma-delta T-cell lymphoma is recorded as a differential
  diagnosis, not as a subtype.

  Frequency figures in this entry are strongly ascertainment-dependent and the
  cohorts are not interchangeable. HAVCR2 carrier fraction ranges from about
  51% in an unselected Korean national cohort to about 86% in a Thai paediatric
  series; HLH frequency ranges from 17% in the adult-weighted EORTC series to
  68% in that same paediatric series. Both extremes are recorded with their
  cohort so that neither is read as the disease-wide number.

  No prevalence rate is recorded because none has been published; the only
  quantitative anchor is SPTCL's share of non-Hodgkin lymphoma diagnoses.
review_notes: >-
  Most of the reference cache committed alongside this entry comes from the
  deep-research run's own citation-validation pass rather than from curation.
  Those files are kept because the report that cites them is committed; they are
  not evidence for anything in the entry. This is repository housekeeping rather
  than disease content, which is why it sits here and not in `notes`.
📚

References & Deep Research

Deep Research

1
Claude Code
Subcutaneous Panniculitis-like T-cell Lymphoma (SPTCL): Comprehensive Research Report
claude-haiku-4-5-20251001, claude-sonnet-5 44 citations 2026-08-29T14:48:59.369706

Subcutaneous Panniculitis-like T-cell Lymphoma (SPTCL): Comprehensive Research Report

1. Disease Information

Overview: Subcutaneous panniculitis-like T-cell lymphoma (SPTCL) is a rare, primary cutaneous peripheral T-cell lymphoma composed of clonal cytotoxic αβ CD8+ T cells that infiltrate subcutaneous adipose tissue, mimicking inflammatory panniculitis both clinically and histologically. It accounts for <1% of all non-Hodgkin lymphomas and <1% of peripheral T-cell lymphomas (StatPearls; Clinical Dermatology Review 2024). It was formally distinguished from the more aggressive primary cutaneous γδ T-cell lymphoma in the 2008 WHO-EORTC classification revision — the term SPTCL is now restricted to the αβ-phenotype entity, which carries a comparatively indolent course (StatPearls; PathologyOutlines).

Key identifiers: - OMIM: #618398 — "T-CELL LYMPHOMA, SUBCUTANEOUS PANNICULITIS-LIKE; SPTCL" (notably listed with a germline genetic basis via HAVCR2) - Orphanet: ORPHA:86884 - MONDO: MONDO:0019475 - ICD-10-CM: C86.3 — "Subcutaneous panniculitis-like T-cell lymphoma" - MeSH: Lymphoma, T-Cell, Cutaneous (subcutaneous panniculitis-like subtype)

Synonyms: SPTCL; subcutaneous panniculitic T-cell lymphoma; panniculitis-like T-cell lymphoma (older/broader usage, now split into SPTCL [αβ] and primary cutaneous γδ T-cell lymphoma).

Evidence basis: The literature is predominantly aggregated case series, retrospective cohorts (EORTC Cutaneous Lymphoma Group, French/Japanese/Korean/Chinese multicenter cohorts), and case reports; there is no large prospective trial or population-based registry (e.g., no dedicated SEER coding stratum), so most epidemiologic and outcome figures derive from pooled single- or multi-center series rather than individual EHR-level aggregation.

2. Etiology

Disease causal factors: SPTCL arises from clonal expansion of cytotoxic αβ T cells homing to subcutaneous fat. A major mechanistic driver identified over the last decade is germline loss-of-function mutation in HAVCR2 (encoding the immune checkpoint receptor TIM-3), found in roughly half to 85% of cases depending on cohort/ancestry (Nat Genet 2018; Blood Adv 2019).

Genetic risk factors: - HAVCR2 (TIM-3) germline variants, most notably c.245A>G (p.Tyr82Cys) — enriched in patients of East Asian and Polynesian ancestry on a shared founder haplotype — and c.291A>G (p.Ile97Met), more common in European-ancestry patients. Both cause TIM-3 protein misfolding and loss of plasma-membrane expression (Nat Genet 2018). - A 2024 Japanese cohort (Okamura et al., Cancer Science) found HAVCR2^Y82C in 51.0% of patients, associated with younger age of onset, HLH development, and shorter relapse-free survival; TET2 recurrent mutations were also identified, while UNC13D, PIAS3, KMT2D mutations were enriched in HAVCR2-wild-type cases (Cancer Sci 2024; PMC11531942). - HAVCR2^Y82C tumors show transcriptional enrichment for IL6-JAK-STAT3 and TNF-α/NF-κB signaling. - Homozygous/biallelic HAVCR2 mutation has been documented even in pediatric sporadic (non-familial) SPTCL (PMID 34398459).

Environmental/associated risk factors: No specific infectious, occupational, or toxin exposure is established as causal. Autoimmune disease co-occurs in ~20% of cases, most notably systemic lupus erythematosus (SLE), at a rate exceeding background population prevalence — some patients present on a histologic/clinical continuum with lupus erythematosus panniculitis (LEP) (Clinical Dermatology Review 2024; molecular overlap study PMID 33966586).

Protective factors: None specifically established in the literature.

Gene-environment interaction: The prevailing model is that germline HAVCR2 loss-of-function lowers the threshold for macrophage/dendritic-cell inflammasome activation (see Mechanism, below); a superimposed trigger (infection, immune stimulation) is hypothesized to precipitate the hyperinflammatory/HLH phenotype, though a specific triggering exposure has not been consistently identified.

3. Phenotypes

Phenotype Type Frequency/Notes Suggested HP term
Subcutaneous nodules/plaques Physical sign Cardinal finding; typically multiple, on extremities and trunk HP:0031477 (Subcutaneous nodule)
Erythematous skin lesions Sign Common HP:0010783 (Erythema)
Painless (or occasionally tender) lesions Symptom Variable; usually painless but can be tender/pruritic
Fever Symptom Common, especially with HLH HP:0001945 (Fever)
Hepatosplenomegaly Sign Seen with HLH complication HP:0001433 / HP:0001744
Pancytopenia/bicytopenia Lab abnormality ~72.7% of HLH-complicated cases (general HLH cohort data) HP:0001873 (Thrombocytopenia), HP:0001899 (Leukopenia), HP:0001903 (Anemia)
Hyperferritinemia Lab abnormality ~95% of HLH-complicated cases HP:0012156 (Elevated serum ferritin, closest available; consider laboratory abnormality mapping)
Hypertriglyceridemia Lab abnormality ~52.5% of HLH cases HP:0002155 (Hypertriglyceridemia)
Hypofibrinogenemia Lab abnormality ~30.8% of HLH cases HP:0011900 (or related coagulation abnormality term)
Lymphadenopathy Sign Uncommon (helps distinguish from nodal PTCL) HP:0002716
Weight loss/B symptoms Symptom Variable HP:0004325
Hemophagocytic lymphohistiocytosis (HLH) Complication/syndrome 15–20% of cases; major prognostic determinant HP:0005517 (Hemophagocytosis)

Onset: Median age of presentation is reported variably across cohorts — roughly 30–46 years depending on series, with a female predominance; ~20% of cases occur in patients <20 years old, including infants (Dove Medical Press pediatric case series; PMC5660631 — 8-month-old infant case).

Progression/course: Classically indolent, relapsing-remitting cutaneous disease without extracutaneous spread in most cases; a minority develop HLH, which is associated with rapid deterioration and markedly worse prognosis. Upper-extremity involvement has been reported as an independent poor-prognostic clinical feature (EORTC study, Blood 2008;111:838).

Quality of life impact: Not systematically studied with validated instruments (EQ-5D/SF-36) in the literature reviewed; morbidity is driven primarily by recurrent cutaneous lesions and, in the HLH subset, systemic multi-organ dysfunction.

4. Genetic/Molecular Information

Causal/predisposition gene: - HAVCR2 (hgnc:18437; encodes TIM-3), 5q33.3. Germline biallelic (homozygous or compound heterozygous) or, in some series, monoallelic loss-of-function variants are strongly associated with SPTCL, particularly the HLH-complicated phenotype. OMIM entry #618398 frames SPTCL as having a defined germline genetic contribution via HAVCR2.

Key variants: - c.245A>G, p.Tyr82Cys (Y82C) — founder variant in East Asian/Polynesian populations; most frequently reported pathogenic allele (up to ~51% of an all-Japanese cohort) (Cancer Sci 2024). - c.291A>G, p.Ile97Met (I97M) — predominant in European-ancestry patients (Nat Genet 2018). - Both are missense, loss-of-function variants causing protein misfolding and failure of TIM-3 surface trafficking (functionally near-null alleles). - Zygosity: Homozygous or compound heterozygous germline genotypes correlate with more severe/HLH phenotypes; heterozygous carriage alone appears insufficient in some models, consistent with recessive inheritance for the HLH-prone phenotype, though case reports of a single confirmed homozygous 14-year-old female patient exist (PMID 34398459). - Somatic co-mutations: recurrent somatic TET2 mutations (epigenetic regulator); UNC13D, PIAS3, KMT2D mutations enriched in HAVCR2-wild-type tumors, suggesting at least partially distinct molecular subgroups (PMC11531942). - Enrichment of IL6-JAK-STAT3 and TNF-α/NF-κB transcriptional signatures in HAVCR2-mutant tumors provides rationale for JAK-inhibitor therapy (see Treatment).

Variant classification: HAVCR2 Y82C and I97M are generally reported as pathogenic/likely pathogenic loss-of-function alleles per functional (protein misfolding/trafficking) assays; population frequency in gnomAD is low but the Y82C founder allele shows regional enrichment in East Asian/Pacific populations.

Somatic vs. germline: The disease-defining HAVCR2 variants are germline (present in non-tumor tissue), distinguishing the genetic mechanism of SPTCL from typical somatically-driven lymphomas; additional somatic mutations (TET2, etc.) likely cooperate in clonal T-cell transformation.

Epigenetics: Limited direct data; TET2 (a DNA-demethylation enzyme) recurrent mutation implicates epigenetic dysregulation as a contributing somatic event, analogous to its role in other T-cell lymphomas (e.g., AITL, PTCL-NOS).

Chromosomal abnormalities: No recurrent SPTCL-specific translocation or aneuploidy has been established as a defining feature; TCR gene rearrangement (clonal) is used diagnostically rather than as a structural chromosomal marker.

Suggested gene/ontology terms: HGNC gene: hgnc:18437 (HAVCR2); GO biological process candidates: "negative regulation of inflammasome activation" (custom/at present no single precise GO ID exists but see GO:0043525-adjacent processes for regulation of neuron apoptosis is irrelevant — better: GO:0032621 "interleukin-18 production," GO:0032621/GO:0002218 "activation of innate immune response").

5. Environmental Information

No specific toxin, occupational, radiation, dietary, or lifestyle exposure has been established as causally linked to SPTCL in the literature surveyed. No infectious agent (viral, bacterial, fungal, or parasitic) has been consistently implicated as an etiologic trigger, in contrast to some other T/NK-cell lymphomas (e.g., EBV in extranodal NK/T-cell lymphoma). One differential-diagnosis pitfall paper does note a peripheral T-cell lymphoma NOS case with HAVCR2 compound heterozygous mutation that was EBV-positive, but this represents a related/overlapping entity rather than an established SPTCL trigger (PMC9539911). No established gene-environment interaction data exist beyond the hypothesis that an unidentified inflammatory trigger unmasks HLH in HAVCR2-deficient hosts.

6. Mechanism / Pathophysiology

Causal chain (proposed model): 1. Germline HAVCR2 loss-of-function → TIM-3 protein misfolds and fails to reach the macrophage/dendritic-cell/T-cell plasma membrane. 2. Loss of TIM-3 inhibitory signaling on macrophages/dendritic cells removes a brake on the TLR–NF-κB pathway, ATP release, K+ efflux, and reactive oxygen species (ROS) production (Frontiers Immunology case report). 3. This lowers the threshold for NLRP3 inflammasome activation, driving excess IL-1β/IL-18 production and macrophage hyperactivation — mechanistically linking TIM-3 deficiency to both the panniculitic tissue infiltrate and, when uncontrolled, systemic hemophagocytic lymphohistiocytosis. 4. In parallel, clonal cytotoxic αβ CD8+ T cells (perforin/granzyme B/TIA-1–expressing) infiltrate and "rim" individual adipocytes within the subcutaneous fat lobule, driving adipocyte apoptosis, karyorrhexis, and fat necrosis — the histologic hallmark ("rimming"). 5. Somatic cooperating mutations (TET2 and others) and enrichment of IL-6/JAK/STAT3 and TNF-α/NF-κB signaling programs are proposed to support clonal T-cell survival/expansion.

Cellular processes: Cytotoxic T-cell–mediated apoptosis of adipocytes; macrophage/histiocyte hyperactivation and hemophagocytosis (engulfment of erythrocytes, leukocytes, platelets, and their precursors) in the HLH-complicated subset; chronic granulomatous-pattern fat necrosis.

Protein dysfunction: TIM-3 (HAVCR2 product) misfolding/loss of surface expression is the central molecular lesion identified to date; this is a loss-of-function immune-checkpoint defect rather than a classic oncogenic driver mutation.

Immune system involvement: Central to pathogenesis — SPTCL sits at the intersection of lymphomagenesis and autoinflammation/autoimmunity, given (a) the ~20% co-occurrence with autoimmune disease (especially SLE), (b) the checkpoint-deficiency mechanism causing innate immune hyperactivation, and (c) the frequent secondary HLH.

Tissue damage mechanisms: Direct cytotoxic T-cell killing of adipocytes; secondary necroinflammatory fat necrosis; in HLH, systemic cytokine-storm–mediated multi-organ injury (hepatic, marrow, splenic).

Suggested GO/CL terms: - GO:0097191 (extrinsic apoptotic signaling pathway) / GO:0001909 (leukocyte-mediated cytotoxicity) - GO:0002218 (activation of innate immune response); GO:0032621 (interleukin-18 production) - CL:0000625 (CD8-positive, alpha-beta T cell); CL:0000913 (effector memory CD8-positive, alpha-beta T cell); CL:0000439 (professional antigen-presenting cell) for macrophages/dendritic cells involved in NLRP3-driven hyperinflammation - CL:0000136 (fat cell/adipocyte) as the injured target cell population

Molecular profiling: RNA-sequencing/whole-exome sequencing studies (discovery cohorts of ~8 patients plus larger validation cohorts) have characterized the HAVCR2-mutant transcriptional signature (IL6-JAK-STAT3, TNF-NF-κB pathway enrichment) (PMC11531942; Blood Adv 2021, PMID 34535012). No large-scale single-cell, spatial transcriptomic, or proteomic datasets specific to SPTCL were identified in this search.

7. Anatomical Structures Affected

  • Primary organ/tissue: Subcutaneous adipose tissue (panniculus), most often of the extremities (especially lower legs/thighs) and trunk; face is less commonly involved.
  • Secondary involvement (HLH-complicated disease): Liver, spleen, bone marrow (hemophagocytosis), lymph nodes (uncommon primary involvement — nodal disease is atypical and should prompt reconsideration of the diagnosis).
  • Tissue/cell level: Subcutaneous fat lobules; cytotoxic CD8+ αβ T lymphocytes infiltrating and rimming individual adipocytes; histiocytes/macrophages (hemophagocytosis in marrow/spleen/liver when HLH supervenes).
  • Subcellular level: Plasma membrane trafficking defect of TIM-3 (HAVCR2 product) in macrophages/dendritic cells/T cells; cytotoxic granule (perforin/granzyme B) machinery in the neoplastic T cells.
  • Suggested UBERON terms: UBERON:0002190 (subcutaneous adipose tissue); UBERON:0002107 (liver); UBERON:0002106 (spleen); UBERON:0002371 (bone marrow).
  • Laterality: Typically bilateral, multifocal nodules rather than strictly unilateral disease.

8. Temporal Development

  • Onset: Can occur across the age spectrum, from infancy to older adulthood; median onset reported between ~30–46 years across cohorts, with ~20% of cases in patients <20 years old.
  • Onset pattern: Typically insidious — gradual appearance of subcutaneous nodules over weeks to months; HLH, when it develops, can have an acute/subacute onset superimposed on chronic cutaneous disease.
  • Progression: Chronic, relapsing-remitting cutaneous course in most patients (indolent, "stable/fluctuating" pattern) without extracutaneous dissemination; a subset (15–20%) develops HLH, which follows a rapidly progressive, life-threatening course.
  • Remission: Spontaneous resolution of individual nodules can occur, but disease-free cure without treatment is not the norm; treatment-induced remission (immunosuppressive therapy achieving complete response in up to 85% of treated patients in some series) is well documented.
  • Disease duration: Chronic, often lifelong tendency to relapse in the non-HLH subset; HLH episodes are acute, life-threatening events requiring urgent intervention.

9. Inheritance and Population

Epidemiology: SPTCL is exceedingly rare — accounting for <1% of all peripheral T-cell lymphomas and <1% of non-Hodgkin lymphomas overall. No dedicated national/SEER-level incidence figure specific to SPTCL was identified; it is generally described only through case-series aggregation.

Inheritance pattern (genetic subset): Where germline biallelic HAVCR2 loss-of-function is present, the pattern is consistent with autosomal recessive predisposition to the HLH-complicated phenotype (homozygous or compound heterozygous genotype associated with more severe disease); however, most reported cases are considered clinically sporadic even when the causal germline variant is identified (i.e., "sporadic" at the clinical-family level but molecularly germline/heritable) (Blood Adv 2019).

Penetrance/expressivity: Incompletely characterized; not all HAVCR2-mutant carriers develop SPTCL or HLH, implying incomplete penetrance and a likely requirement for additional somatic or environmental cooperating factors.

Founder effect: The HAVCR2 p.Tyr82Cys (Y82C) variant occurs on a shared founder haplotype in patients of East Asian and Polynesian ancestry; p.Ile97Met is more prevalent in patients of European ancestry — a clear population-genetic/geographic stratification (Nat Genet 2018).

Demographics: Reports consistently note a female predominance. Pediatric and adolescent presentation is well documented (~20% of cases <20 years).

10. Diagnostics

Histopathology (gold standard): Deep incisional/excisional skin biopsy (not superficial punch) showing lobular panniculitis with atypical lymphocytes "rimming" individual adipocytes, karyorrhexis, fat necrosis, and cytophagic histiocytes (fat/lymphocyte engulfment by benign histiocytes — "beanbag cells") without epidermal involvement (PathologyOutlines; PMC2965923).

Immunohistochemistry: Neoplastic cells are CD3+, CD8+, βF1+ (αβ TCR), CD4−, CD56−, CD30−, with expression of cytotoxic markers TIA-1, granzyme B, perforin. An elevated Ki-67 proliferation index ("Ki-67 hotspots") among CD8+ rimming lymphocytes helps distinguish SPTCL from lupus panniculitis (PMID 26796503; PMID 29742552).

Molecular/genetic testing: Clonal TCR gene rearrangement (T-cell receptor gamma/beta) by PCR supports diagnosis. Germline HAVCR2 sequencing (Sanger or targeted NGS panel) is increasingly used, especially in cases with HLH or pediatric presentation, given the high mutation prevalence.

Differential diagnosis — SPTCL vs. lupus erythematosus panniculitis (LEP): LEP favors epidermal changes, reactive lymphoid follicles with germinal centers, mixed infiltrate with plasma cells, CD123+ plasmacytoid dendritic cell clusters, polyclonal TCR rearrangement, and low Ki-67; SPTCL favors monomorphous CD8+ rimming infiltrate, high Ki-67 "hotspots," and clonal TCR rearrangement. LEP and SPTCL can overlap and coexist in the same patient, and molecular studies of ~208 genes have shown genuine overlap cases exist on a disease spectrum (PMID 33966586; PMID 26796503).

Differential diagnosis — SPTCL vs. primary cutaneous γδ T-cell lymphoma: γδ phenotype (rather than αβ) predicts a much more aggressive course with frequent HLH, ulceration, and extracutaneous spread; distinguishing requires TCR-δ/βF1 immunostaining. Increased reactive γδ T cells within an otherwise αβ SPTCL is a described diagnostic pitfall (MD Anderson publication).

Imaging: ¹⁸F-FDG PET/CT is used for staging and to assess extracutaneous involvement/treatment response (Frontiers Oncology, 11 patients).

HLH work-up: When SPTCL is diagnosed, screen for HLH using the HLH-2004 criteria (≥5 of 8): fever, splenomegaly, cytopenia in ≥2 lineages, hypertriglyceridemia and/or hypofibrinogenemia, hemophagocytosis on marrow/spleen/node biopsy, low/absent NK-cell cytotoxicity, hyperferritinemia, elevated soluble CD25 (sIL-2R).

Staging: Cutaneous lymphoma TNMB (tumor, node, metastasis, blood) staging is applied per NCCN Cutaneous Lymphomas guidelines to define disease burden and guide skin-directed vs. systemic therapy selection.

11. Outcome/Prognosis

Survival: Overall prognosis is favorable for the αβ (SPTCL proper) phenotype, with reported 5-year overall survival of 85–91% and 3-year OS around 85.2% in some cohorts (PMC8523605; EORTC study Blood 2008;111:838).

HLH impact: HLH complicates 15–20% of cases and is the single most important adverse prognostic factor, reducing 5-year OS to roughly 46%. HAVCR2-mutant (especially Y82C) cases show higher HLH incidence, greater HLH severity, and shorter relapse-free survival.

Other adverse prognostic factors: Upper-extremity lesion location has been associated with worse outcome (EORTC study).

Recurrence: Cutaneous relapse is common even after complete response to immunosuppressive therapy; ongoing surveillance is required.

Cause of death (when it occurs): Predominantly related to uncontrolled HLH/multi-organ failure or infection, rather than direct tumor-related organ failure from cutaneous disease itself.

12. Treatment

First-line (non-HLH disease): Immunosuppressive therapy — systemic corticosteroids, alone or combined with low-dose methotrexate or cyclosporine A — is now generally preferred over cytotoxic polychemotherapy for uncomplicated disease, achieving complete response in up to 85% of treated patients in some cohorts. A French cohort found complete remission in 81.2% with immunosuppressive drugs vs. only 28.5% with polychemotherapy, and progression in 6.2% vs. 42.8% respectively (Acta Derm Venereol). Sustained CR rates were broadly comparable between chemotherapy (64%) and immunosuppressive therapy (55%) in another analysis.

  • Treatment_term: NCIT:C15986 (Pharmacotherapy) with therapeutic_agent bound to CHEBI terms for prednisone/prednisolone, methotrexate (CHEBI:44185), and ciclosporin (CHEBI:4031). Cyclosporine has also been proposed as upfront therapy even in aggressive-feature disease (PMC12778365).

Radiotherapy: Used for localized/solitary lesions (NCIT:C15313, Radiation Therapy).

Chemotherapy: Multiagent regimens (e.g., CHOP-based) reserved for patients with HLH at presentation, or who progress on/are refractory to immunosuppressive therapy (NCIT:C15632, Chemotherapy). Pralatrexate has shown a significant response in a case of HLH-complicated SPTCL (PMC12593427).

HLH-directed therapy: Ruxolitinib (JAK1/2 inhibitor) has demonstrated efficacy in SPTCL-associated HLH, mechanistically rational given the IL6-JAK-STAT3 pathway enrichment in HAVCR2-mutant disease (Blood Adv 2020). Etoposide-containing HLH-directed regimens (e.g., HLH-94/HLH-2004-style, or CHOEP) have been used in severe/refractory HLH cases, sometimes bridging to autologous hematopoietic stem cell transplantation (PMID 23995110 — BFM-NHL/ALL-90 regimen plus autologous PBSCT).

Surgical/reconstructive: Dermal matrix (e.g., Integra®) reconstruction has been reported for extensive cutaneous defects in a multimodal management case (MDPI).

Experimental/novel: Emapalumab (anti-IFN-γ monoclonal antibody, approved for primary HLH) is mechanistically plausible for HLH-complicated SPTCL given interferon-driven macrophage activation, though this search did not surface SPTCL-specific published outcomes data for it.

Treatment algorithm summary: | Clinical scenario | Preferred approach | |---|---| | Uncomplicated cutaneous SPTCL | Corticosteroids ± methotrexate/cyclosporine (immunosuppressive-first) | | Localized/solitary lesion | Radiotherapy | | Refractory to immunosuppression | Multiagent chemotherapy | | SPTCL + HLH | Chemotherapy/HLH-directed regimen ± ruxolitinib; consider stem cell transplant in severe/refractory cases |

13. Prevention

No established primary prevention strategy exists, as no modifiable environmental or infectious trigger has been identified. Secondary prevention/early detection centers on prompt deep biopsy of persistent subcutaneous nodules to avoid diagnostic delay (frequently misdiagnosed initially as benign panniculitis, cellulitis, or lupus panniculitis) and on proactive HLH surveillance (ferritin, triglycerides, fibrinogen, CBC) in confirmed SPTCL patients, particularly those with known HAVCR2 mutations, to enable rapid initiation of HLH-directed therapy. Genetic counseling may be considered for families with a germline HAVCR2 variant, given the (incompletely penetrant) autosomal-recessive-pattern association with HLH-complicated disease, though no formal cascade-screening guideline was identified in this search. No vaccine or prophylactic pharmacologic strategy is described.

14. Other Species / Natural Disease

No naturally occurring veterinary correlate of SPTCL specifically was identified in this search (unlike some other lymphoma subtypes with described companion-animal analogs in OMIA). TIM-3 (Havcr2) biology has been studied in mouse models: conditional deletion of TIM-3 in murine dendritic cells leads to ROS accumulation and NLRP3 inflammasome activation, and murine Tim-3-deficiency models have been used to demonstrate loss of the TLR–NF-κB inhibitory brake in macrophages, mechanistically recapitulating the human hyperinflammatory phenotype (Frontiers Immunology). These are gene-function models of the HAVCR2 pathway rather than spontaneous SPTCL-mimicking disease models. Orthologous gene: mouse Havcr2 (Tim-3), NCBI Gene.

15. Model Organisms

  • Genetic (knockout/conditional) mouse models: Tim-3 (Havcr2) conditional knockout mice, particularly dendritic-cell– and macrophage-specific deletion models, recapitulate loss of TIM-3–mediated inhibition of TLR-NF-κB signaling and NLRP3 inflammasome hyperactivation — informative for the HLH/hyperinflammatory arm of SPTCL pathophysiology, but these are gene-pathway models rather than tumor-forming SPTCL models.
  • Limitations: No described mouse model recapitulates the full clonal cytotoxic-T-cell lymphomagenesis phenotype of human SPTCL; existing models address only the innate-immune/inflammasome consequence of TIM-3 loss, not lymphoma development itself.
  • Cell-line/in vitro models: Patient-derived macrophages from HAVCR2-mutant HLH-SPTCL patients have been used ex vivo to demonstrate lowered inflammasome activation thresholds and increased inflammatory cytokine release, providing direct human functional validation complementing the mouse data.
  • No organoid, iPSC-derived, or zebrafish SPTCL models were identified in this search.

Summary Table: Suggested Ontology Bindings

Domain Suggested term
Disease MONDO:0019475; OMIM:618398; ORPHA:86884; ICD-10: C86.3
Causal gene hgnc:18437 (HAVCR2)
Cell type CL:0000625 (CD8+ αβ T cell); CL:0000136 (adipocyte); CL:0000235 (macrophage)
Anatomy UBERON:0002190 (subcutaneous adipose tissue); UBERON:0002106 (spleen); UBERON:0002107 (liver)
Key phenotype HP:0031477 (subcutaneous nodule); HP:0001945 (fever); HP:0005517 (hemophagocytosis); HP:0002155 (hypertriglyceridemia)
Treatment agent CHEBI:4031 (ciclosporin); CHEBI:44185 (methotrexate); NCIT:C15986 (Pharmacotherapy); NCIT:C15632 (Chemotherapy); NCIT:C15313 (Radiation Therapy)

Sources

Reference Validation

Checked with linkml-reference-validator 0.2.1.

Outcome Count
References checked 25
Resolved 24
Unresolved (possible confabulation) 1
Unverifiable 0
References weighed for topical relevance 24
On topic 14
Off topic 0

Unresolved references

These identifiers did not resolve to a record and may be fabricated. A lookup that failed for transport reasons is indistinguishable from one that failed because the record does not exist, so spot-check before acting on them:

  • DOI:10.1182/bloodadvances.2021004562/476947/Genetic-profiles-of-subcutaneous-panniculitis-like (2 mentions) - Identifier did not resolve to a record

Term Validation

Checked with linkml-term-validator 0.4.5, through the ols: adapter.

Outcome Count
Terms checked 36
Resolved 33
Unresolved (possible confabulation) 0
Obsolete 1
Unverifiable 2
Terms whose name was checked 20
Terms named correctly 13
Terms named as a different term 5
Terms whose name is worth a second look 2

Terms the report names something else

These identifiers resolve, so nothing about them looks wrong, and the ontology calls them something unrelated to what the report calls them. That usually means the identifier is not the one the sentence needs:

  • HP:0031477 (2 mentions) - the report calls it "Subcutaneous nodule"; HP calls it obsolete Abnormal mitral valve morphology
  • HP:0012156 (1 mention) - the report calls it "Elevated serum ferritin, closest available; consider laboratory abnormality mapping"; HP calls it Hemophagocytosis
  • HP:0002716 (1 mention) - the report calls it "Uncommon (helps distinguish from nodal PTCL)"; HP calls it Lymphadenopathy
  • HP:0004325 (1 mention) - the report calls it "Variable"; HP calls it Decreased body weight
  • HP:0005517 (2 mentions) - the report calls it "Hemophagocytosis"; HP calls it T-cell lymphoma/leukemia

Obsolete terms

These terms are real but deprecated. Citing one is not a fabrication; it does mean the report is naming something the ontology has retired:

  • HP:0031477 (obsolete Abnormal mitral valve morphology) (2 mentions) - replaced by HP:0001633

Terms whose name is worth a second look

The report's name for these is recognisably related to the term's own name without being one of them. A loose paraphrase reads the same way as a citation of the wrong sibling term - and so does a related synonym, which the ontology records precisely because it names something adjacent rather than the same thing - so these are listed rather than judged:

  • CL:0000439 (1 mention) - the report calls it "professional antigen-presenting cell"; CL calls it prolactin secreting cell
  • CL:0000136 (2 mentions) - the report calls it "fat cell/adipocyte"; CL calls it adipocyte

Prefixes with no resolver

Terms carrying these prefixes were not checked either way, because no configured ontology covers them. An unrecognised prefix may name an ontology this run could not reach as easily as one that does not exist, so nothing here is evidence of fabrication: ORPHA, OMIM.