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1
Inheritance
3
Pathophys.
5
Phenotypes
3
Pathograph
3
Genes
1
Treatments
3
References
1
Deep Research
👪

Inheritance

1
Autosomal dominant inheritance HP:0000006
Congenital hypofibrinogenemia is caused by heterozygous loss-of-function mutations in FGA, FGB, or FGG; a single pathogenic allele roughly halves fibrinogen output, producing the quantitative deficiency characteristic of this disorder.
Autosomal dominant inheritance
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"Hypofibrinogenemia is generally caused by heterozygosity for these mutations."
The review states that hypofibrinogenemia is caused by heterozygosity for null or hypomorphic fibrinogen gene mutations, confirming autosomal dominant (heterozygous) inheritance.

Pathophysiology

3
Reduced Fibrinogen Synthesis
Heterozygosity for fibrinogen null or hypomorphic alleles (large deletions, frameshift, nonsense, splice-site, or secretion-impairing missense mutations) reduces the amount of normal fibrinogen produced and secreted by hepatocytes, producing proportionally low circulating fibrinogen.
hepatocyte link
Show evidence (2 references)
PMID:29316703 SUPPORT Human Clinical
"Hypofibrinogenemia is generally caused by heterozygosity for these mutations."
The review attributes hypofibrinogenemia to heterozygosity for the fibrinogen-deficiency mutation classes, i.e. a loss-of-function mechanism.
PMID:29316703 SUPPORT Human Clinical
"causative mutations can be divided into two main classes: null mutations with no protein production at all and mutations producing abnormal protein chains which are retained inside the cell"
The review describes the two causative-mutation classes underlying quantitative fibrinogen deficiency.
Impaired Fibrin Clot Formation
Low plasma fibrinogen limits fibrin polymerization, so clot-based coagulation assays are prolonged in proportion to the residual fibrinogen level.
blood coagulation, fibrin clot formation link ↓ DECREASED
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"In hypofibrinogenemia, standard clotting assays are variably prolonged according to the circulating fibrinogen level."
The review notes that clotting assays are prolonged in proportion to the circulating fibrinogen level in hypofibrinogenemia.
Bleeding Diathesis
The bleeding tendency is mild and strongly correlated with the residual coagulant fibrinogen level; many patients are asymptomatic, and bleeding is typically provoked by trauma or surgery rather than spontaneous.
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"a mean fibrinogen activity level of at least 0.7 g/L protected from spontaneous bleeding, while patients with a level above 1.0 g/L did not experience bleeds"
The retrospective cohort data quantify the level-dependence of the bleeding phenotype in fibrinogen deficiency.

Pathograph

Use the checkboxes to hide or show graph categories. Hover nodes for evidence and cross-linked metadata.
Pathograph: causal mechanism network for Congenital Hypofibrinogenemia Interactive directed graph showing how pathophysiology mechanisms, phenotypes, genetic factors and variants, experimental models, environmental triggers, and treatments relate through causal and linked edges.

Phenotypes

5
Blood 2
Abnormal Bleeding Abnormal bleeding (HP:0001892)
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"In afibrinogenemia bleeding is the main symptom, whereas in hypofibrinogenemia patients are more frequently asymptomatic."
The review contrasts the frequently asymptomatic course of hypofibrinogenemia with the bleeding-dominated phenotype of afibrinogenemia.
Menorrhagia Menorrhagia (HP:0000132)
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"hypofibrinogenemic women are also affected by menorrhagia"
The review reports menorrhagia among hypofibrinogenemic women, dependent on fibrinogen level.
Prenatal and Birth 1
Obstetrical complications Abnormality of prenatal development or birth (HP:0001197)
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"such as recurrent placenta abruption, suggesting insufficient fibrinogen to sustain placenta development"
The review directly reports obstetrical complications including recurrent placental abruption in hypofibrinogenemic women, attributing these to insufficient fibrinogen for placental integrity.
Other 2
Hypofibrinogenemia VERY_FREQUENT Hypofibrinogenemia (HP:0011900)
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"hypofibrinogenemia is characterized by fibrinogen levels lower than 1.5 g/L"
The review defines hypofibrinogenemia by reduced circulating fibrinogen, making low fibrinogen an obligate feature of the disorder.
Persistent Bleeding After Trauma Persistent bleeding after trauma (HP:0001934)
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"the bleeding phenotype is usually linked to trauma, surgery"
The review notes that symptomatic bleeding in hypofibrinogenemia is usually provoked by trauma or surgery.
🧬

Genetic Associations

3
FGA (Causative)
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"encoded by the fibrinogen gene cluster FGB, FGA, and FGG on human chromosome 4"
The review identifies FGA as one of the three fibrinogen chain-encoding genes whose mutations cause quantitative fibrinogen deficiency.
FGB (Causative)
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"encoded by the fibrinogen gene cluster FGB, FGA, and FGG on human chromosome 4"
The review identifies FGB as one of the three fibrinogen chain-encoding genes whose mutations cause quantitative fibrinogen deficiency.
FGG (Causative)
Show evidence (1 reference)
PMID:29316703 SUPPORT Human Clinical
"more than 200 different mutations have been identified as accounting for afibrinogenemia or hypofibrinogenemia"
The review documents that mutations across the three fibrinogen genes, including FGG, account for afibrinogenemia and hypofibrinogenemia.
💊

Treatments

1
Fibrinogen Replacement Therapy
Action: Pharmacotherapy NCIT:C15986
Agent: fibrinogen concentrate
Fibrinogen supplementation (fibrinogen concentrate) for on-demand management of bleeding episodes or perioperative/peripartum prophylaxis; asymptomatic patients with adequate residual levels generally require no treatment.
Show evidence (1 reference)
PMID:36055263 SUPPORT Human Clinical
"Fibrinogen supplementation is the cornerstone of bleeding management in fibrinogen disorders."
The review identifies fibrinogen supplementation as the mainstay of bleeding management in congenital fibrinogen disorders.
{ }

Source YAML

click to show
name: Congenital Hypofibrinogenemia
creation_date: '2026-05-16T00:00:00Z'
updated_date: '2026-05-18T19:00:00Z'
category: Genetic
parents:
- Bleeding Disorder
- Coagulation Disorder
disease_term:
  preferred_term: congenital hypofibrinogenemia
  term:
    id: MONDO:0015096
    label: familial hypofibrinogenemia
description: >-
  Congenital hypofibrinogenemia is a quantitative (Type I) congenital fibrinogen
  disorder caused by mutations in the fibrinogen genes FGA, FGB, or FGG, leading
  to proportionally reduced functional and antigenic plasma fibrinogen
  (typically <1.5 g/L). In the simple form, the defect is a loss-of-function:
  heterozygosity for null or hypomorphic alleles roughly halves fibrinogen
  output, the liver is structurally normal, and the bleeding tendency is mild
  and strongly dependent on the residual fibrinogen level (patients are
  frequently asymptomatic). This entry covers the simple quantitative form; the
  mechanistically distinct hepatic fibrinogen storage disease (toxic
  gain-of-function FGG variants causing hepatocyte ER aggregation) is treated as
  a separate entity.
prevalence:
- population: General population
  notes: >-
    Inherited fibrinogen disorders are rare; a precise population prevalence for
    congenital hypofibrinogenemia is not well established, and many heterozygous
    carriers are detected incidentally.
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Inherited disorders of fibrinogen are rare."
    explanation: >-
      The review states that inherited fibrinogen disorders, including
      quantitative defects such as hypofibrinogenemia, are rare.
pathophysiology:
- name: Reduced Fibrinogen Synthesis
  description: >-
    Heterozygosity for fibrinogen null or hypomorphic alleles (large deletions,
    frameshift, nonsense, splice-site, or secretion-impairing missense
    mutations) reduces the amount of normal fibrinogen produced and secreted by
    hepatocytes, producing proportionally low circulating fibrinogen.
  cell_types:
  - preferred_term: hepatocyte
    term:
      id: CL:0000182
      label: hepatocyte
  downstream:
  - target: Impaired Fibrin Clot Formation
    description: >-
      Reduced circulating fibrinogen limits the substrate available for
      thrombin-mediated conversion to fibrin.
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Hypofibrinogenemia is generally caused by heterozygosity for these mutations."
    explanation: >-
      The review attributes hypofibrinogenemia to heterozygosity for the
      fibrinogen-deficiency mutation classes, i.e. a loss-of-function mechanism.
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "causative mutations can be divided into two main classes: null mutations with no protein production at all and mutations producing abnormal protein chains which are retained inside the cell"
    explanation: >-
      The review describes the two causative-mutation classes underlying
      quantitative fibrinogen deficiency.
- name: Impaired Fibrin Clot Formation
  description: >-
    Low plasma fibrinogen limits fibrin polymerization, so clot-based
    coagulation assays are prolonged in proportion to the residual fibrinogen
    level.
  biological_processes:
  - preferred_term: blood coagulation, fibrin clot formation
    modifier: DECREASED
    term:
      id: GO:0072378
      label: blood coagulation, fibrin clot formation
  downstream:
  - target: Bleeding Diathesis
    description: >-
      Impaired fibrin clot formation predisposes to a level-dependent bleeding
      tendency.
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "In hypofibrinogenemia, standard clotting assays are variably prolonged according to the circulating fibrinogen level."
    explanation: >-
      The review notes that clotting assays are prolonged in proportion to the
      circulating fibrinogen level in hypofibrinogenemia.
- name: Bleeding Diathesis
  description: >-
    The bleeding tendency is mild and strongly correlated with the residual
    coagulant fibrinogen level; many patients are asymptomatic, and bleeding is
    typically provoked by trauma or surgery rather than spontaneous.
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "a mean fibrinogen activity level of at least 0.7 g/L protected from spontaneous bleeding, while patients with a level above 1.0 g/L did not experience bleeds"
    explanation: >-
      The retrospective cohort data quantify the level-dependence of the
      bleeding phenotype in fibrinogen deficiency.
phenotypes:
- name: Hypofibrinogenemia
  category: Hematologic
  frequency: VERY_FREQUENT
  description: >-
    Defining laboratory feature: proportionally reduced functional and
    antigenic plasma fibrinogen, conventionally below 1.5 g/L.
  phenotype_term:
    preferred_term: Hypofibrinogenemia
    term:
      id: HP:0011900
      label: Hypofibrinogenemia
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "hypofibrinogenemia is characterized by fibrinogen levels lower than 1.5 g/L"
    explanation: >-
      The review defines hypofibrinogenemia by reduced circulating fibrinogen,
      making low fibrinogen an obligate feature of the disorder.
- name: Abnormal Bleeding
  category: Hematologic
  description: >-
    Bleeding is variable and level-dependent; hypofibrinogenemic patients are
    frequently asymptomatic, with symptomatic bleeding usually provoked by
    trauma or surgery.
  phenotype_term:
    preferred_term: Abnormal bleeding
    term:
      id: HP:0001892
      label: Abnormal bleeding
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "In afibrinogenemia bleeding is the main symptom, whereas in hypofibrinogenemia patients are more frequently asymptomatic."
    explanation: >-
      The review contrasts the frequently asymptomatic course of
      hypofibrinogenemia with the bleeding-dominated phenotype of afibrinogenemia.
- name: Persistent Bleeding After Trauma
  category: Hematologic
  description: >-
    In symptomatic patients, bleeding is typically linked to trauma or surgery
    rather than occurring spontaneously.
  phenotype_term:
    preferred_term: Persistent bleeding after trauma
    term:
      id: HP:0001934
      label: Persistent bleeding after trauma
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "the bleeding phenotype is usually linked to trauma, surgery"
    explanation: >-
      The review notes that symptomatic bleeding in hypofibrinogenemia is
      usually provoked by trauma or surgery.
- name: Menorrhagia
  category: Hematologic
  description: >-
    Depending on the fibrinogen level, affected women may experience heavy
    menstrual bleeding.
  phenotype_term:
    preferred_term: Menorrhagia
    term:
      id: HP:0000132
      label: Menorrhagia
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "hypofibrinogenemic women are also affected by menorrhagia"
    explanation: >-
      The review reports menorrhagia among hypofibrinogenemic women, dependent
      on fibrinogen level.
- name: Obstetrical complications
  category: Reproductive
  description: >-
    Hypofibrinogenemic women are at risk of obstetrical complications
    including recurrent placental abruption and pregnancy loss, reflecting
    the requirement of fibrinogen for placental integrity and fetal-maternal
    vascular development throughout pregnancy.
  phenotype_term:
    preferred_term: Obstetrical complications including recurrent placental abruption
    term:
      id: HP:0001197
      label: Abnormality of prenatal development or birth
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "such as recurrent placenta abruption, suggesting insufficient fibrinogen to sustain placenta development"
    explanation: >-
      The review directly reports obstetrical complications including recurrent
      placental abruption in hypofibrinogenemic women, attributing these to
      insufficient fibrinogen for placental integrity.
inheritance:
- name: Autosomal dominant inheritance
  inheritance_term:
    preferred_term: Autosomal dominant inheritance
    term:
      id: HP:0000006
      label: Autosomal dominant inheritance
  description: >-
    Congenital hypofibrinogenemia is caused by heterozygous loss-of-function
    mutations in FGA, FGB, or FGG; a single pathogenic allele roughly halves
    fibrinogen output, producing the quantitative deficiency characteristic
    of this disorder.
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Hypofibrinogenemia is generally caused by heterozygosity for these mutations."
    explanation: >-
      The review states that hypofibrinogenemia is caused by heterozygosity
      for null or hypomorphic fibrinogen gene mutations, confirming
      autosomal dominant (heterozygous) inheritance.
genetic:
- name: FGA
  gene_term:
    preferred_term: FGA
    term:
      id: hgnc:3661
      label: FGA
  association: Causative
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "encoded by the fibrinogen gene cluster FGB, FGA, and FGG on human chromosome 4"
    explanation: >-
      The review identifies FGA as one of the three fibrinogen
      chain-encoding genes whose mutations cause quantitative fibrinogen deficiency.
- name: FGB
  gene_term:
    preferred_term: FGB
    term:
      id: hgnc:3662
      label: FGB
  association: Causative
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "encoded by the fibrinogen gene cluster FGB, FGA, and FGG on human chromosome 4"
    explanation: >-
      The review identifies FGB as one of the three fibrinogen
      chain-encoding genes whose mutations cause quantitative fibrinogen deficiency.
- name: FGG
  gene_term:
    preferred_term: FGG
    term:
      id: hgnc:3694
      label: FGG
  association: Causative
  evidence:
  - reference: PMID:29316703
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "more than 200 different mutations have been identified as accounting for afibrinogenemia or hypofibrinogenemia"
    explanation: >-
      The review documents that mutations across the three fibrinogen genes,
      including FGG, account for afibrinogenemia and hypofibrinogenemia.
treatments:
- name: Fibrinogen Replacement Therapy
  description: >-
    Fibrinogen supplementation (fibrinogen concentrate) for on-demand
    management of bleeding episodes or perioperative/peripartum prophylaxis;
    asymptomatic patients with adequate residual levels generally require no
    treatment.
  treatment_term:
    preferred_term: Pharmacotherapy
    term:
      id: NCIT:C15986
      label: Pharmacotherapy
    therapeutic_agent:
    - preferred_term: fibrinogen concentrate
      term:
        id: NCIT:C81126
        label: Fibrinogen Human
  evidence:
  - reference: PMID:36055263
    supports: SUPPORT
    evidence_source: HUMAN_CLINICAL
    snippet: "Fibrinogen supplementation is the cornerstone of bleeding management in fibrinogen disorders."
    explanation: >-
      The review identifies fibrinogen supplementation as the mainstay of
      bleeding management in congenital fibrinogen disorders.
references:
- reference: PMID:30076675
  title: 'Diagnosis and classification of congenital fibrinogen disorders: communication from the SSC of the ISTH.'
  findings: []
- reference: PMID:36055263
  title: One Hundred Years of Congenital Fibrinogen Disorders.
  findings: []
- reference: PMID:29316703
  title: Clinical Consequences and Molecular Bases of Low Fibrinogen Levels.
  findings: []
notes: >-
  Scope note: this entry models the simple quantitative (Type I) form
  (loss-of-function, liver structurally normal). Hepatic fibrinogen storage
  disease (HFSD) — toxic gain-of-function FGG missense variants near
  polymerization pocket "hole a" causing hepatocyte endoplasmic-reticulum
  fibrinogen aggregation and a distinct hepatopathy — is mechanistically
  distinct and is curated as a separate entity (see issue #2727). Tracker: #2727.
📚

References & Deep Research

References

3
Diagnosis and classification of congenital fibrinogen disorders: communication from the SSC of the ISTH.
No top-level findings curated for this source.
One Hundred Years of Congenital Fibrinogen Disorders.
No top-level findings curated for this source.
Clinical Consequences and Molecular Bases of Low Fibrinogen Levels.
No top-level findings curated for this source.

Deep Research

1
Scanner
Scanner Research Synthesis: Congenital Hypofibrinogenemia (Simple Quantitative Form)
claude-sonnet-4-6 2026-05-18T00:00:00Z

Scanner Research Synthesis: Congenital Hypofibrinogenemia (Simple Quantitative Form)

This report is based on cached reference abstracts available in references_cache/.


Disease Identity

  • Preferred name: Congenital Hypofibrinogenemia (simple quantitative form)
  • MONDO: MONDO:0015096 (familial hypofibrinogenemia)
  • ISTH classification: Type I (quantitative) congenital fibrinogen disorder
  • OMIM: 202400 (afibrinogenemia, autosomal recessive); hypofibrinogenemia is the heterozygous form with partial deficiency
  • Note: This entry covers the simple LOF form only. Hepatic Fibrinogen Storage Disease (HFSD/HHHS), caused by specific FGG missense variants driving hepatocyte ER aggregation, is a mechanistically distinct entity treated separately.

Core Pathophysiology

Genetic Mechanism

Congenital hypofibrinogenemia is caused by heterozygous loss-of-function mutations in one of three fibrinogen chain genes: FGA (Aα chain), FGB (Bβ chain), or FGG (γ chain), clustered at chromosome 4q28.

Causative mutation classes (PMID:29316703): 1. Null mutations — complete loss of expression from one allele (large deletions, frameshift, nonsense, splice-site variants) 2. Hypomorphic/secretion-impairing missense mutations — protein produced but mis-folded or retained intracellularly, reducing secretion

Because fibrinogen is a heterohexamer (2×Aα + 2×Bβ + 2×γ), loss of one chain prevents normal hexamer assembly from that allele. Heterozygosity reduces hepatic output by approximately 50%, resulting in circulating fibrinogen levels between 0.5–1.5 g/L (normal range: 2–4 g/L).

Molecular Pathway

  1. Heterozygous LOF allele (FGA/FGB/FGG)
  2. Reduced fibrinogen hexamer assembly and secretion by hepatocytes
  3. Low circulating fibrinogen (hypofibrinogenemia; Fg:C <1.5 g/L)
  4. Limited substrate for thrombin-mediated fibrin polymerization
  5. Impaired fibrin clot formation
  6. Level-dependent bleeding diathesis (typically mild; prothrombotic Fg:C >1.0 g/L is broadly protective)

Key Liver Biology

Fibrinogen is an acute-phase protein synthesized exclusively by hepatocytes (CL:0000182). All three chains are co-expressed, assembled in the ER, and secreted as intact hexamers. In the simple quantitative form, liver morphology is normal (no intracellular aggregation), distinguishing this from HFSD.


Clinical Phenotype

Severity Spectrum

Severity correlates directly with residual fibrinogen level (PMID:29316703): - Fg:C ≥1.0 g/L: Generally asymptomatic; most heterozygous carriers fall here - Fg:C 0.7–1.0 g/L: Mild-to-moderate bleeding risk, typically provoked - Fg:C <0.7 g/L: Increased spontaneous bleeding risk; approaches afibrinogenemia spectrum

Major Phenotypes

Hematologic: - Hypofibrinogenemia (obligate, defining) — HP:0011900 - Abnormal bleeding (variable severity) — HP:0001892 - Persistent bleeding after trauma/surgery — HP:0001934

Reproductive (females): - Menorrhagia — HP:0000132 (level-dependent) - Obstetrical complications including recurrent placental abruption — reflects fibrinogen requirement for placental integrity. Fibrinogen is necessary for cytotrophoblast spreading at 4–6 weeks gestation and fetal-maternal vascular development (PMID:29316703).

Laboratory Findings

  • Prolonged PT and aPTT (proportional to fibrinogen level)
  • Reduced plasma fibrinogen by both Clauss clotting assay and immunologic antigen assay (both low, distinguishing from dysfibrinogenemia where ratio differs)
  • Thromboelastography: reduced clot amplitude and firmness

Genetics

Gene HGNC Chain Mutation classes
FGA hgnc:3661 Null and missense; >200 variants described
FGB hgnc:3662 Null and missense
FGG hgnc:3694 γ Null and missense (non-polymerization-pocket missense; HFSD-causing γ variants are excluded from this entry)

Inheritance: Autosomal dominant (heterozygous LOF). Afibrinogenemia (biallelic null) is autosomal recessive. Hypofibrinogenemia is the heterozygous carrier state of autosomal recessive afibrinogenemia alleles, and also arises de novo.


Treatment

Fibrinogen replacement (on-demand and prophylactic): - Fibrinogen concentrate (e.g., Haemocomplettan/RiaSTAP; NCIT:C81126 Fibrinogen Human) is the therapeutic cornerstone (PMID:36055263) - Targets: Fg:C ≥1.0 g/L (general hemostasis), ≥1.5–2.0 g/L perioperatively, ≥2.0 g/L peripartum - Cryoprecipitate (contains fibrinogen, FVIII, vWF, FXIII) is an alternative where concentrate is unavailable - Antifibrinolytics (tranexamic acid) are useful adjuncts for minor bleeds and dental procedures

Asymptomatic management: - Many patients with Fg:C >1.0 g/L require no prophylactic treatment - Awareness of obstetric risks and perioperative prophylaxis planning are important for female patients


Key References

PMID Authors Title Key content
29316703 de Moerloose et al. (2018) Clinical Consequences and Molecular Bases of Low Fibrinogen Levels Main review covering pathophysiology, phenotype, obstetric complications
36055263 Casini et al. (2022) One Hundred Years of Congenital Fibrinogen Disorders Classification evolution, fibrinogen concentrate, 100-year review
30076675 Casini et al. (2018) Diagnosis and classification of congenital fibrinogen disorders ISTH SSC classification framework

Scope Note

This entry models the simple quantitative (Type I, LOF, liver-normal) form of hypofibrinogenemia. Two mechanistically distinct entities in the congenital fibrinogen disorder family are treated separately: - Afibrinogenemia: biallelic null (AR); more severe - Hepatic Fibrinogen Storage Disease (HFSD): gain-of-toxic-function FGG missense → hepatocyte ER aggregation → hepatopathy (see sibling entry)

Tracker issue: #2727.